Myotonic Dystrophy Clinical Trials in Richmond, Virginia

8 recruitingRichmond, Virginia

Showing 18 of 8 trials

Recruiting
Phase 1Phase 2

A Study to Investigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 55 Years of Age With Non-congenital Myotonic Dystrophy Type 1

Myotonic Dystrophy
Sanofi32 enrolled9 locationsNCT06844214
Recruiting
Phase 1Phase 2

Safety, Tolerability, Pharmacodynamic, Efficacy, and Pharmacokinetic Study of DYNE-101 in Participants With Myotonic Dystrophy Type 1

Myotonic Dystrophy Type 1 (DM1)
Dyne Therapeutics116 enrolled17 locationsNCT05481879
Recruiting
Phase 1Phase 2

A Phase 1/2 Study of VX-670 in Adult Participants With Myotonic Dystrophy 1 (DM1)

Myotonic Dystrophy Type 1 (DM1)
Vertex Pharmaceuticals Incorporated44 enrolled26 locationsNCT06185764
Recruiting
Phase 1Phase 2

Study of ATX-01 in Participants With DM1

Myotonic Dystrophy 1
ARTHEx Biotech S.L.56 enrolled12 locationsNCT06300307
Recruiting

Trial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy Extension

Myotonic DystrophyCongenital Myotonic DystrophyChildhood Myotonic Dystrophy
Virginia Commonwealth University200 enrolled1 locationNCT06747884
Recruiting

DMCRN-02-001: Assessing Pediatric Endpoints in DM1

Congenital Myotonic DystrophyCDM
Virginia Commonwealth University50 enrolled5 locationsNCT05224778
Recruiting

Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)

Myotonic Dystrophy 1DM1
Virginia Commonwealth University700 enrolled17 locationsNCT03981575
Recruiting
Phase 2Phase 3

Safety and Efficacy of Tideglusib in Congenital or Childhood Onset Myotonic Dystrophy

Congenital Myotonic Dystrophy
AMO Pharma Limited76 enrolled14 locationsNCT05004129