NET Clinical Trials in Paris
10 recruitingParis, France
Showing 1–10 of 10 trials
Recruiting
Phase 2Phase 3
A Study of the Efficacy and Safety of Danicamtiv in Participants With Symptomatic Genetic and Familial Dilated Cardiomyopathy
Symptomatic Genetic Dilated Cardiomyopathy
Kardigan, Inc.332 enrolled33 locationsNCT07210723
Recruiting
Phase 1
A Study of the Safety, Tolerability, Pharmacokinetics, and Immunogenicity of BCX17725
Netherton Syndrome
BioCryst Pharmaceuticals78 enrolled12 locationsNCT06539507
Recruiting
Characterization and Contribution of Genome-wide DNA Methylation (DNA Methylation Episignatures) in Rare Diseases With Prenatal Onset
Congenital MalformationRare Fetal Genetic Diseases
Assistance Publique - Hôpitaux de Paris63 enrolled1 locationNCT06475651
Recruiting
Molecular Diagnosis of Systemic Autoinflammatory Diseases
Genetic DiseaseMolecular Pathway DeregulationSomatic Mutation+2 more
Institut National de la Santé Et de la Recherche Médicale, France300 enrolled1 locationNCT05364294
Recruiting
Natural History of Type 1 Interferonopathies: Insights From a European Cohort
Genetic DiseaseAutoimmune DiseasesNeurological Diseases or Conditions+1 more
Imagine Institute500 enrolled32 locationsNCT07040774
Recruiting
Not Applicable
Biocollection of Rare Pediatric-onset of Autoimmune and Autoinflammatory Diseases
Genetic DiseaseAutoimmune DiseasesAutoinflammatory Disease+1 more
Hospices Civils de Lyon400 enrolled13 locationsNCT06435468
Recruiting
Not Applicable
Effectiveness of PKP vs DSAEK in Terms of 2-year Postoperative Visual Acuity in Advanced BPK
Bullous Pseudophakic KeratopathyPenetrating Keratoplasty
Centre Hospitalier Régional Metz-Thionville334 enrolled11 locationsNCT06818747
Recruiting
Not Applicable
COsegregation of VARiants in Panel of Genes
Genetic PredispositionGene Mutation-Related Cancer
Institut Curie3,500 enrolled57 locationsNCT01689584
Recruiting
Acute Myeloid Leukemia At Initial Diagnosis and/or Relapse in Children, Teenagers and Young Adults: Molecular Profiling, Multidrug Testing and MSC Interaction Studies
Acute Myeloid LeukemiaGenetic Predisposition to Disease
Assistance Publique - Hôpitaux de Paris500 enrolled28 locationsNCT05772559
Recruiting
Biomarker Research in Inherited Movement Disorders
Spinocerebellar AtaxiasInherited Movement DisordersHyperkinetic Disorders
Assistance Publique - Hôpitaux de Paris4,000 enrolled1 locationNCT05034172