Phase 2 Ornithine Transcarbamylase Deficiency Clinical Trials
3 recruitingPhase 2
What is a Phase 2 trial?
Phase 2 trials evaluate whether a treatment works for a specific condition and further assess its safety. These studies typically enroll several hundred participants and provide preliminary data on effectiveness.
Showing 1–3 of 3 trials
Recruiting
Phase 1Phase 2
An Open-label Study to Investigate ECUR-506 in Male Babies Less Than 9 Months of Age With Neonatal Onset OTC Deficiency
Ornithine Transcarbamylase DeficiencyOrnithine Transcarbamylase Deficiency DiseaseUrea Cycle Disorders, Inborn+1 more
iECURE, Inc.20 enrolled12 locationsNCT06255782
Recruiting
Phase 2
A Study to Evaluate the Pharmacodynamics and Safety of ARCT-810 in Participants With OTCD
Ornithine Transcarbamylase DeficiencyOTC DeficiencyOTCD
Arcturus Therapeutics, Inc.9 enrolled1 locationNCT06488313
Recruiting
Phase 1Phase 2
Halting Ornithine Transcarbamylase Deficiency With Recombinant AAV in ChildrEn
Ornithine Transcarbamylase Deficiency
University College, London12 enrolled1 locationNCT05092685