Early Phase 1 X-Linked Clinical Trials

3 recruitingEarly Phase 1

What is a Early Phase 1 trial?

Early Phase 1 trials are the earliest stage of testing in humans. These small studies focus on how a drug is processed in the body and how it affects the body, often enrolling just a handful of participants to establish initial safety data.

Showing 1–3 of 3 trials

Recruiting

Early Phase 1

Expanded Access Protocol Using CD3+/CD19+ Depleted PBSC

LeukemiaInborn Errors of MetabolismBone Marrow Failure Syndromes+2 more

Children's Hospital of Philadelphia100 enrolled1 locationNCT02356653

Recruiting

Early Phase 1

Safety and Efficacy of a Single Subretinal Injection of JWK002 Gene Therapy in Subjects With X-linked Retinoschisis(XLRS)

X-linked Retinoschisis

West China Hospital12 enrolled1 locationNCT06345898

Recruiting

Early Phase 1

Gene Therapy for Subjects With RPGR Mutation-associated X-linked Retinitis Pigmentosa

X-Linked Retinitis Pigmentosa

Frontera Therapeutics18 enrolled2 locationsNCT05874310