RecruitingPhase 3NCT04221035

High-Risk Neuroblastoma Study 2 of SIOP-Europa-Neuroblastoma (SIOPEN)


Sponsor

Gustave Roussy, Cancer Campus, Grand Paris

Enrollment

800 participants

Start Date

Nov 5, 2019

Study Type

INTERVENTIONAL

Conditions

Summary

This is an international multicenter, open-label, randomized phase III trial including three sequential randomizations to assess efficacy of induction and consolidation chemotherapies and radiotherapy for patients with high-risk neuroblastoma.


Eligibility

Max Age: 21 Years

Plain Language Summary

Simplified for easier understanding

This study is testing new treatment approaches for children and young people with high-risk neuroblastoma, a serious cancer that forms in nerve tissue, often in the adrenal glands or abdomen. The goal is to find more effective treatment combinations to improve survival. **You may be eligible if...** - Your child (or you) has been diagnosed with high-risk neuroblastoma - The diagnosis is either widespread (Stage M) or involves a specific gene change (MYCN amplification) - Treatment has not yet started, or started very recently (within 21 days of one chemotherapy cycle) - Your child is over 12 months old with widespread disease, or any age with MYCN gene amplification - You have provided informed consent, with appropriate assent from the child **You may NOT be eligible if...** - Your child has already received multiple rounds of chemotherapy - Your child's neuroblastoma does not meet the high-risk criteria - You are unwilling or unable to use contraception during treatment (for patients of childbearing age) - You are currently breastfeeding Talk to your doctor to see if this trial is right for you.

This summary was AI-generated to explain the trial in plain language. It is not medical advice. Always discuss eligibility with your doctor before enrolling in a clinical trial.

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Interventions

DRUGVincristine

1.5 mg/m2 (max dose 2 mg)

DRUGCarboplatin

750 mg/m2

DRUGEtoposide

175 mg/m2

DRUGVindesine

3 mg/m2/day (max dose 6 mg)

DRUGDacarbazine

200 mg/m2/day

DRUGIfosfamide

1500 mg/m2/day

DRUGDoxorubicin

30 mg/m2/dose

DRUGBusulfan

\< 9kg: 1.0 mg/kg/dose 9 kg to \< 16 kg : 1.2 mg/kg/dose 16 kg to 23 kg : 1.1 mg/kg/dose \>23 kg to 34 kg: 0.95 mg/kg/dose \>34 kg: 0.8 mg/kg/dose Infusion IV over 2 hours Administration every 6 hours for a total of 16 doses

DRUGMelphalan

140 mg/m2/dose IV short infusion (15'), at least 24 h after the last busulfan dose

DRUGThiotepa

300 mg/m2/day over 2 hours

RADIATIONRadiotherapy

21.6 Gy 21.6 Gy + boost de 14.4 Gy

DRUGDinutuximab Beta

Patients \>12 kg are dosed based on the BSA: 10 mg/m\^2/day Patients ≤ 12 kg are dosed according to their body weight: 0.33 mg/kg/day

DRUGCisplatin

80 mg/m2/24h

DRUGTemozolomide 100 MG

100 mg/m²/Day

DRUGIrinotecan

50 mg/m²/jour de J0 à J4

DRUGCyclophosphamid

Cyclophosphamide has been demonstrated to have a cytostatic effect in many tumour types. The active metabolites of cyclophosphamide are alkylating agents which transfer alkyl groups to DNA during the process of cell division, thus preventing normal synthesis of DNA.


Locations(142)

Sydney children Hospital

Sydney, Randwick, Australia

Children's Cancer Centre, Monash Children's Hospital

Clayton, Australia

Oncology/Haematology Department, Perth Children's Hospital

Nedlands, Australia

Children's Cancer & Haematology Services, John Hunter Children's Hospital

New Lambton Heights, Australia

Australian and New Zealand Children's Hematology/oncology Group

Sydney, Australia

sydney children Hospital

Sydney, Australia

Cancer Centre for Children, The Children's Hospital

Westmead, Australia

Medical University Graz

Graz, Austria

Landeskrankenhaus-Universitätsklinikum Innsbruck

Innsbruck, Austria

Kepler Universitatsklinikum Linz

Linz, Austria

Universitastsklinikum Salzburg

Salzburg, Austria

St Anna'S Children Hospital

Vienna, Austria

Hôpital Universitaire des Enfants Reine Fabiola (ULB)

Brussels, Belgium

Cliniques Universitaires Saint-Luc (UCL)

Brussels, Belgium

University Hospital Gent

Ghent, Belgium

University Hospitals Leuven

Leuven, Belgium

CHR Citadelle

Liège, Belgium

University Hospital Motol

Prague, Prague, Czechia

Klinika dětské onkologie FN Brno

Brno, Czechia

Aarhus University Hospital

Aarhus, Denmark

Department of Paediatrics and Adolescent Medicine, Rigshospitalet

Copenhagen, Denmark

The Hans Christian Andersen Children's Hospital, University of Southern Denmark

Odense, Denmark

New Children's Hospital, Helsinki University Hospital, Helsinki and Uusimaa Hospital District

Helsinki, Finland

Kuopio University Hospital

Kuopio, Finland

Oulu University Hospital

Oulu, Finland

Tampere University Hospital

Tampere, Finland

Turku University Hospital

Turku, Finland

Gustave Roussy

Villejuif, Val De Marne, France

CHU d'AMIENS

Amiens, France

CHU angers

Angers, France

CHU-Pôle Médico-Chirurgical de l'Enfant et l'Adolescant

Besançon, France

CHU Bordeaux

Bordeaux, France

Groupe Hospitalier Pellegrin - Chu - Bordeaux

Bordeaux, France

CHU Brest

Brest, France

CHU Brest - Hôpital du Morvan

Brest, France

Centre François Baclesse

Caen, France

CHU de Caen

Caen, France

CHU Estaing

Clermont-Ferrand, France

Centre Georges-François Leclerc

Dijon, France

Hopital d'enfants Marechal de lattre

Dijon, France

Hôpital Couple-Enfant CHU de Grenoble

Grenoble, France

Chu de La Reunion - St Denis

La Réunion, France

centre Oscar lambert

Lille, France

Hôpital de la Mère et de l'Enfant - CHU Limoges

Limoges, France

Centre Léon Berard

Lyon, France

hopital la Timone

Marseille, France

CHRU Nancy-Hôpital Brabois Enfant

Nancy, France

Institut de cancérologie de Loraine

Nancy, France

Centre Antoine Lacassagne

Nice, France

CHU Nice-Hôpital d'Archet

Nice, France

Hôpital Armand Trousseau

Paris, France

institut Curie

Paris, France

CHU Poitiers

Poitiers, France

Hôpital Américain -CHU Reims

Reims, France

Centre Eugène Marquis

Rennes, France

CHU Rennes

Rennes, France

Hôpital des Enfants - CHU Rouen

Rouen, France

CHU Saint Etienne

Saint-Etienne, France

Institut de cancérologie de l'Ouest - Sité René Gauducheau

Saint-Herblain, France

CHU Haute Pierre

Strasbourg, France

Institut de Cancérologie Strasbourg

Strasbourg, France

Hopital des enfants-CHU Toulouse

Toulouse, France

IUCT Oncopole

Toulouse, France

CHU Tours Hôpital Clocheville

Tours, France

charite universitatsmedizin Berlin

Berlin, Germany

Uniklinik Köln, Klinik und Poliklinik für Kinder und Jugendmedizin

Cologne, Germany

Children's General Hospital "I AGHIA SOFIA"

Athens, Greece

Children's General Hospital "P. & A. KYRIAKOU"

Athens, Greece

"MITERA" Private, General, Obstetrics - Gynaecology, Paediatric Clinic S.A.

Athens, Greece

Children's General Hospital "AGHIA SOFIA"

Athens, Greece

University General Hospital of Heraklion (UnGHH)

Heraklion, Greece

University General Hospital of Thessaloniki "AHEPA"

Thessaloniki, Greece

General Hospital of Thessaloniki "IPPOKRATIO"

Thessaloniki, Greece

RAMBAM Medical Center

Haifa, Israel

A.O.U Policlinico di Bari

Bari, Italy

Spedali civili Ospedale Dei Bambini Oncoematologia pediatrica e TMO

Brescia, Italy

policlinico rodolico San marco

Catania, Italy

Azienda ospedaliero universtaria Anna Meyer

Florence, Italy

instituto Giannina Gaslini genova

Genova, Italy

IRCCS "Istituto Giannina Gaslini"

Genova, Italy

Azienda Policlinico di Modena

Modena, Italy

Azienda ospedaliero universitaria di Parma

Parma, Italy

Policlino San matteo di Pavia

Pavia, Italy

U.O Pediatria, SS Oncoematologia pediatrica

Rimini, Italy

IRCCS Burlo Garoflo oncoematologia

Trieste, Italy

U.O.C oncoematologia pediatrica ospedale Donna Bambino

Verona, Italy

Vilnius University Hospital Santaros Klinikos

Vilnius, Lithuania

National Cancer Institute

Vilnius, Lithuania

Universitair Medisch Centrum Groningen

Groningen, Netherlands

Princess Maxima center

Utrecht, Netherlands

Haukeland University Hospital

Haukeland, Norway

Oslo University Hospital

Oslo, Norway

University Hospital Northern Norway, Tromsoe

Tromsø, Norway

St Olavs Hospital,

Trondheim, Norway

Children's University Hospital Banská Bystrica

Banská Bystrica, Slovakia

NÚDCH- National Institute of Children's Diseases,

Bratislava, Slovakia

Children's University Hospital Košice

Košice, Slovakia

University medical center Ljubljana, University Children's Hospital Ljubljana, Slovenia

Ljubljana, Slovenia

Hospital Universitario Son Espases

Balea, Spain

Hospital Universitario Vall D´Hebron

Barcelona, Spain

Hospital Universitario Cruces

Cruces, Spain

Hospital Clínico Universitario Virgen de la Arrixaca

El Palmar, Spain

Hospital Universitario Infantil Niño Jesús

Madrid, Spain

Hospital Universitario La Paz

Madrid, Spain

Hospital Regional Universitario de Málaga

Málaga, Spain

Hospital Universitario Donostia

San Sebastián, Spain

Hospital Clínico Universitario de Santiago

Santiago de Compostela, Spain

Hospital Universitario Virgen del Rocío

Seville, Spain

Hospital Universitario Politécnico de La FE

Valencia, Spain

Sahlgrenska University Hospital

Gothenburg, Sweden

Linköping University Hospital

Linköping, Sweden

Skåne University Hospital

Lund, Sweden

Karolinska University Hospital, Stockholm

Stockholm, Sweden

Norrland University Hospital

Umeå, Sweden

Uppsala University Hospital

Uppsala, Sweden

Kantonsspital Aarau AG Klinik für Kinder und Jugendliche

Aarau, Switzerland

Universitäts-Kinderspital beider Basel (UKBB)

Basel, Switzerland

Ospedale San Giovanni Pediatria, Emato-oncologia pediatrica

Bellinzona, Switzerland

Inselspital, Universitätsklinik für Kinderheilkunde

Bern, Switzerland

HUG Hôpitaux Universitaires de Genève Unité d'Hémato-Oncologie Pédiatrique

Geneva, Switzerland

CHUV - Centre Hospitalier Universitaire Vaudois

Lausanne, Switzerland

Luzerner Kantonsspital, Kinderspital pädiatrische Hämatologie/Onkologie

Lucerne, Switzerland

Ostschweizer Kinderspital Hämatologie/Onkologie Claudiusstrasse 6

Sankt Gallen, Switzerland

Division of Pediatric Oncology Universitäts-Kinderspital Zürich

Zurich, Switzerland

Royal Aberdeen Children's Hospital

Aberdeen, United Kingdom

Royal Belfast Hospital for Sick Children

Belfast, United Kingdom

Birmingham children's Hospital

Birmingham, United Kingdom

University Hospitals Birmingham Queen Elisabeth Hospital(UHB)

Birmingham, United Kingdom

University Hospitals Bristol and Weston NHS Foundation Trust

Bristol, United Kingdom

Addenbrookes Hospital, Cambridge

Cambridge, United Kingdom

Noah's Ark Children's Hospital for Wales - Cardiff

Cardiff, United Kingdom

Royal Hospital for Sick Children - Edinburgh

Edinburgh, United Kingdom

Royal Hospital for Children Glasgow

Glasgow, United Kingdom

Leeds General Infirmary

Leeds, United Kingdom

Alder Hey Children's Hospital - Liverpool

Liverpool, United Kingdom

Great Ormond Street Hospital - London

London, United Kingdom

Royal Manchester Children's Hospital

Manchester, United Kingdom

Royal Victoria Infirmary, Newcastle

Newcastle, United Kingdom

Nottingham Children's Hospital

Nottingham, United Kingdom

Sheffield Children's Hospital

Sheffield, United Kingdom

Southampton General Hospital

Southampton, United Kingdom

Royal Marsden Hospital

Sutton, United Kingdom

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