RecruitingPhase 2NCT05646381

A Multicenter Trial Assessing the Impact of Lipoprotein(a) Lowering With Pelacarsen (TQJ230) on the Progression of Calcific Aortic Valve Stenosis

A Randomized Double-blind, Placebo-controlled, Multicenter Trial Assessing the Impact of Lipoprotein(a) Lowering With Pelacarsen (TQJ230) on the Progression of Calcific Aortic Valve Stenosis [Lp(a)FRONTIERS CAVS]


Sponsor

Novartis Pharmaceuticals

Enrollment

502 participants

Start Date

Mar 7, 2024

Study Type

INTERVENTIONAL

Conditions

Summary

The purpose of this study is to evaluate the efficacy, safety and tolerability of pelacarsen (TQJ230) administered subcutaneously once monthly compared to placebo in slowing the progression of calcific aortic valve stenosis.


Eligibility

Min Age: 50 YearsMax Age: 80 Years

Inclusion Criteria4

  • Male and female ≥50 to \<80 years of age at Screening Part II
  • Lp(a) ≥175 nmol/L at the screening visit, measured at the Central laboratory
  • Mild or moderate calcific aortic valve stenosis
  • At the randomization visit, participant must be optimally treated for existing CV risk factors

Exclusion Criteria8

  • Severe calcific aortic valve stenosis
  • Uncontrolled hypertension
  • History of malignancy of any organ system
  • History of hemorrhagic stroke or other major bleeding
  • Platelet count ≤ LLN
  • Active liver disease or hepatic dysfunction
  • Significant kidney disease
  • Pregnant or nursing women

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Interventions

DRUGPelacarsen (TQJ230) 80mg

Pelacarsen (TQJ230) 80mg

DRUGMatching placebo

Matching placebo


Locations(136)

Heart Center Research Llc

Huntsville, Alabama, United States

Cardiovascular Res Found

Beverly Hills, California, United States

National Heart Institute

Beverly Hills, California, United States

Flourish Clinical Resrch Covin

Covina, California, United States

Valley Clinical Trials

Northridge, California, United States

Stanford University Medical Center

Palo Alto, California, United States

University Of California San Diego

San Diego, California, United States

UC San Francisco Medical Center

San Francisco, California, United States

Excel Medical Clinical Trials LLC

Boca Raton, Florida, United States

Nova Clinical Research LLC

Bradenton, Florida, United States

Flourish Res Acq LLC North Miami

Miami, Florida, United States

Inpatient Research Clinical LLC

Miami Lakes, Florida, United States

Advanced Research for Health Improvement LLC

Naples, Florida, United States

Midwest Heart and Vascular Spec

Overland Park, Kansas, United States

Tufts Medical Center

Boston, Massachusetts, United States

Massachusetts General Hospital

Boston, Massachusetts, United States

Massachusetts General Hospital

Boston, Massachusetts, United States

Brigham and Womens Hosp Harvard Med School

Boston, Massachusetts, United States

Brigham and Womens Hosp Harvard Med School

Boston, Massachusetts, United States

Henry Ford Hospital

Detroit, Michigan, United States

Henry Ford Hospital

Detroit, Michigan, United States

AA Medical Research Center

Flint, Michigan, United States

William Beaumont Hospital

Royal Oak, Michigan, United States

Minneapolis Heart Institute

Minneapolis, Minnesota, United States

University Of Minnesota

Minneapolis, Minnesota, United States

Overlook Medical Center

Summit, New Jersey, United States

Capital Cardiology Associates

Albany, New York, United States

New York Presbyterian Hospital

New York, New York, United States

Icahn School of Med at Mt Sinai

New York, New York, United States

Strong Memorial Hospital

Rochester, New York, United States

Wake Forest University Baptist Medical Center

Winston-Salem, North Carolina, United States

Lindner Ctr At The Christ Hosp

Cincinnati, Ohio, United States

Ohio State University

Columbus, Ohio, United States

Perelman School of Medicine

Philadelphia, Pennsylvania, United States

Orion Medical

Houston, Texas, United States

Virginia Heart

Falls Church, Virginia, United States

Carient Heart and Vascular

Manassas, Virginia, United States

Novartis Investigative Site

Innsbruck, Tyrol, Austria

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Linz, Austria

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Vienna, Austria

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Vienna, Austria

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Genk, Limburg, Belgium

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Yvoir, Namur, Belgium

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Aalst, Oost Vlaanderen, Belgium

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Kortrijk, West-Vlaanderen, Belgium

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Roeselare, West-Vlaanderen, Belgium

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Cambridge, Ontario, Canada

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North York, Ontario, Canada

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Ottawa, Ontario, Canada

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Montreal, Quebec, Canada

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Montreal, Quebec, Canada

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Montreal, Quebec, Canada

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Québec, Quebec, Canada

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Hradec Králové, Czechia

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Jaroměř, Czechia

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Prague, Czechia

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Prague, Czechia

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Prague, Czechia

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Esbjerg, Denmark

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Hvidovre, Denmark

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Roskilde, Denmark

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Viborg, Denmark

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Paris, France

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Paris, France

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Paris, France

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Pessac, France

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Poitiers, France

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Rennes, France

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Frankfurt am Main, Hesse, Germany

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Kaiserslautern, Rhineland-Palatinate, Germany

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Dresden, Saxony, Germany

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Leipzig, Saxony, Germany

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Ahaus, Germany

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Berlin, Germany

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Bonn, Germany

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Essen, Germany

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Hamburg, Germany

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Hamburg, Germany

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Lüneburg, Germany

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Mannheim, Germany

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München, Germany

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Münster, Germany

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Oldenburg, Germany

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Beersheba, Israel

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Haifa, Israel

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Haifa, Israel

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Jerusalem, Israel

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Jerusalem, Israel

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Nahariya, Israel

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Petah Tikva, Israel

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Ramat Gan, Israel

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Tel Aviv, Israel

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Ancona, AN, Italy

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Bergamo, BG, Italy

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Bologna, BO, Italy

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Brescia, BS, Italy

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Caserta, CE, Italy

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Cona, FE, Italy

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Pozzilli, IS, Italy

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Milan, MI, Italy

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Milan, MI, Italy

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Milan, MI, Italy

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Padova, PD, Italy

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Pordenone, PN, Italy

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Amsterdam, North Holland, Netherlands

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Amsterdam, North Holland, Netherlands

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Rotterdam, South Holland, Netherlands

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Rotterdam, South Holland, Netherlands

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Nieuwegein, Utrecht, Netherlands

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Alcabideche, Portugal

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Braga, Portugal

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Coimbra, Portugal

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Vila Nova de Gaia, Portugal

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Cáceres, Extremadura, Spain

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Córdoba, Spain

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Madrid, Spain

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Madrid, Spain

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Madrid, Spain

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Madrid, Spain

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Salamanca, Spain

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Valencia, Spain

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Basel, Switzerland

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Geneva, Switzerland

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Lausanne, Switzerland

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Lugano, Switzerland

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Zurich, Switzerland

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Portadown, Nothern Ireland, United Kingdom

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Edinburgh, United Kingdom

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Leicester, United Kingdom

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Liverpool, United Kingdom

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London, United Kingdom

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London, United Kingdom

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Londonderry, United Kingdom

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Manchester, United Kingdom

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Middlesbrough, United Kingdom

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Tyne and Wear, United Kingdom

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NCT05646381


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