RecruitingPhase 2NCT06046222

Trial of Efficacy and Safety of NS-229 Versus Placebo in Patients With Eosinophilic Granulomatosis With Polyangiitis

A Phase 2, Double-blind, Randomized, Placebo-controlled Study to Investigate the Efficacy and Safety of NS-229 in the Treatment of Eosinophilic Granulomatosis With Polyangiitis


Sponsor

NS Pharma, Inc.

Enrollment

45 participants

Start Date

Dec 20, 2023

Study Type

INTERVENTIONAL

Conditions

Summary

This study will enroll male and female subjects who are 18 years of age or older with Eosinophilic Granulomatosis With Polyangiitis.


Eligibility

Min Age: 18 Years

Inclusion Criteria5

  • Ability to provide written informed consent prior to participation in the study.
  • Male or female subjects aged ≥18 years at the time the informed consent form is signed.
  • Diagnosis of EGPA: Subjects who have been diagnosed with EGPA based on the history or presence of eosinophilia plus at least a history or presence of 2 of additional features of EGPA.
  • Subjects receive background OGC dose of ≥7.5 mg/day with or without stable treatment with Mepolizumab/Benralizumab.
  • Use of adequate contraception.

Exclusion Criteria19

  • Current diagnosis of either granulomatosis with polyangiitis or microscopic polyangiitis
  • Imminently life-threatening EGPA at the time of screening.
  • History or presence of any form of cancer within 5 years prior to screening.
  • Serious liver, renal, blood, or psychiatric disease
  • Severe or clinically significant cardiovascular disease uncontrolled with standard treatment
  • Active systemic infections (including TB, pneumonia, Pneumocystis pneumonia, sepsis, and opportunistic infections)
  • Parasitic infection: Subjects with a known parasitic infestation within 6 months prior to screening.
  • HIV positive status
  • Active hepatitis due to hepatitis B virus or hepatitis C virus
  • Known history or presence of venous thromboembolism/venous thrombotic events (deep vein thrombosis and/or pulmonary embolus)
  • laboratory parameter exclusions:
  • Estimated glomerular filtration rate of \<30 mL/min/1.73 m2 by Chronic Kidney Disease Epidemiology Collaboration equations
  • WBC count \<4 × 109/L
  • Absolute lymphocyte count \<500 cells/mm3
  • Absolute neutrophil count \<1000 cells/mm3
  • Platelet count \<120,000/mm3
  • Hemoglobin \<8 g/dL (\<80 g/L)
  • Subjects who are pregnant, breastfeeding, or planning to become pregnant during the time of study participation
  • History of clinically significant drug or alcohol abuse within the last 6 months

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Interventions

DRUGNS-229

Experimental

DRUGPlacebo

Placebo comparator


Locations(34)

National Jewish Health

Denver, Colorado, United States

Mayo Clinic

Rochester, Minnesota, United States

Cleveland Clinic

Cleveland, Ohio, United States

The Ohio State University Wexner Medical Center

Columbus, Ohio, United States

University of Pennsylvania

Philadelphia, Pennsylvania, United States

Medical University of South Carolina

Charleston, South Carolina, United States

Vanderbilt University Medical Center

Nashville, Tennessee, United States

University of Alberta

Edmonton, Alberta, Canada

St Joseph's Healthcare Hamilton

Hamilton, Ontario, Canada

University of Toronto

Toronto, Ontario, Canada

CHU Nice

Nice, France

Hopital Cochin

Paris, France

Chu Rangueil

Toulouse, France

Medius Kliniken gGmbh

Kirchheim unter Teck, Studienzentrale, Germany

Istituto Auxologico Italiano IRCCS

Milan, Italy

Fondazione Policlinico Universitario Campus Bio-Medico

Roma, Italy

Azienda Provinciale per i Servizi Sanitari Provincia Autonoma Trento

Trento, Italy

Azienda Ospedaliera Universitaria Integrata Verona

Verona, Italy

Chiba University Hospital

Chuo-ku, Chiba-shi, Chiba, Japan

Hospital of the University of Occupational and Environmental Health, Japan

Kitakyushu, Fukuoka, Japan

Hokkaido University Hospital

Sapporo, Hokkaido, Japan

NHO Sagamihara National Hospital

Sagamihara, Kanagawa, Japan

National Hospital Organization Yokohama Medical Center

Yokohama, Kanagawa, Japan

Tohoku University Hospital

Sendai, Miyagi, Japan

Osaka Habikino Medical Center

Habikino, Osaka, Japan

Saitama Medical Center

Kawagoe, Saitama, Japan

Juntendo University Hospital

Bunkyo-ku, Tokyo, Japan

Kyorin University Hospital

Mitaka, Tokyo, Japan

Toho University Omori Medical Center

Ōta-ku, Tokyo, Japan

Complejo Hospitalario Universitario de Santiago de Compostela

Santiago de Compostela, A Coruna, Spain

Complejo Hospitalario de Navarra

Pamplona, Spain

Queen Elizabeth Hospital Birmingham

Edgbaston, Birmingham, United Kingdom

Addenbrookes Hospital

Cambridge, United Kingdom

Royal Berkshire NHS Foundation Trust

Reading, United Kingdom

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NCT06046222


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