RecruitingNCT06214507
Danon Disease Natural History Study
An Observational Study of Genetic Cardiomyopathy, Danon Disease
Sponsor
Rocket Pharmaceuticals Inc.
Enrollment
60 participants
Start Date
Dec 20, 2023
Study Type
OBSERVATIONAL
Conditions
Summary
The goal of this international observational study is to learn about the natural history of Danon disease in male patients (≥8 years of age) and female patients (8 to 50 years of age).
Eligibility
Min Age: 8 Years
Plain Language Summary
Simplified for easier understanding
This clinical trial is studying No intervention for people with danon disease. The study is currently recruiting participants at 13 locations. People eligible for this study include aged 8 Years and older.
This summary was AI-generated to explain the trial in plain language. It is not medical advice. Always discuss eligibility with your doctor before enrolling in a clinical trial.
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Interventions
OTHERNo intervention
No intervention
Locations(15)
View Full Details on ClinicalTrials.gov
For the most up-to-date information, visit the official listing.
NCT06214507
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