RecruitingNCT06795152
Rare Glycogen Storage Diseases Natural History Study
Sponsor
Duke University
Enrollment
200 participants
Start Date
Dec 23, 2024
Study Type
OBSERVATIONAL
Conditions
Summary
The purpose of this study is to collect and study key medical data about several ultra-rare GSDs (Glycogen Storage Diseases) including, but not limited to, GSD types 0a, 0b, VII, X, XII, XIII, XV, PRKAG2 syndrome and Danon disease.
Eligibility
Min Age: 0 YearsMax Age: 90 Years
Plain Language Summary
Simplified for easier understanding
This clinical trial is studying No intervention for people with danon disease, gsd type 0a, and other related conditions. The study is currently recruiting participants at 1 location. People eligible for this study include aged 0 Years to 90 Years.
This summary was AI-generated to explain the trial in plain language. It is not medical advice. Always discuss eligibility with your doctor before enrolling in a clinical trial.
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Interventions
OTHERNo intervention
Observational. Natural history study.
Locations(1)
View Full Details on ClinicalTrials.gov
For the most up-to-date information, visit the official listing.
NCT06795152
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