RecruitingPhase 1NCT06220201

A Study to Evaluate the Safety, Tolerability, Efficacy, and Drug Levels of CC-97540 in Participants With Relapsing Forms of Multiple Sclerosis, Progressive Forms of Multiple Sclerosis or Refractory Myasthenia Gravis (MG) (Breakfree-2)

A Phase 1, Multicenter, Single-arm, Dose-escalation Study of CC-97540 (BMS-986353), CD19-Targeted NEX-T Chimeric Antigen Receptor (CAR) T Cells, Evaluating Safety and Tolerability in Participants With Autoimmune Neurological Diseases: Relapsing Forms of Multiple Sclerosis (RMS), Progressive Forms of Multiple Sclerosis (PMS), or Refractory Myasthenia Gravis (MG).


Sponsor

Juno Therapeutics, Inc., a Bristol-Myers Squibb Company

Enrollment

120 participants

Start Date

Mar 28, 2024

Study Type

INTERVENTIONAL

Conditions

Summary

The purpose of this study is to evaluate the safety, tolerability, efficacy, and drug levels of CC-97540 in participants with Relapsing Forms of Multiple Sclerosis (RMS), Progressive Forms of Multiple Sclerosis (PMS) or Refractory Myasthenia Gravis (MG).


Eligibility

Min Age: 18 YearsMax Age: 60 Years

Inclusion Criteria11

  • \- Relapsing forms of Multiple Sclerosis (RMS) - Cohort 1.
  • i) Participants must have an Expanded Disability Status Scale (EDSS) of ≥ 3.0 and ≤ 5.5.
  • ii) Participants must have a diagnosis of Multiple Sclerosis (MS) with relapsed/refractory MS or conversion to active secondary progressive multiple sclerosis (aSPMS), and worsening of disease within 12 months prior to Screening and while on treatment with a high-efficacy DMT for at least 6 months.
  • \- Progressive forms of MS - Cohort 2.
  • i) Participants must have an EDSS ≥ 3.0 and ≤ 6.0.
  • ii) Participants must have a diagnosis of primary progressive multiple sclerosis (PPMS) that is treatment-resistant or diagnosis of inactive secondary progressive multiple sclerosis (iSPMS).
  • \- Myasthenia Gravis - Cohort 3
  • i)MGFA classification of II-IV at screening
  • ii) Documentation of autoantibodies against AChR or MuSK (historical or at Screening)
  • iii) Refractory disease defined as disease activity on at least 2 immunosuppressants, including steroids, NSIs, or biologics.
  • iv) Has had thymectomy, only if indicated according to current guidelines.

Exclusion Criteria3

  • Cohorts 1 and 2: Participants that cannot complete the 9-Hole Peg Test (9-HPT) in at least 1 hand in \<240 seconds unless extenuating medical conditions unrelated to MS prohibit this.
  • Participants that cannot perform a Timed 25-Foot Walk Test (T25FWT) in \< 150 seconds.
  • Presence of other confounding peripheral nervous system disorders or other disorders that may impact muscle strength (eg, myositis) or cause weakness, stroke, chronic inflammatory demyelinating polyradiculoneuropathy, Lambert-Eaton myasthenic syndrome.

Interventions

DRUGCC-97540

Specified dose on specified days

DRUGFludarabine

Specified dose on specified days

DRUGCyclophosphamide

Specified dose on specified days


Locations(35)

University of Alabama at Birmingham

Birmingham, Alabama, United States

University of California, Irvine

Irvine, California, United States

University of Colorado Anschutz Medical Campus

Aurora, Colorado, United States

Colorado Blood Cancer Institute

Denver, Colorado, United States

Yale-New Haven Hospital

New Haven, Connecticut, United States

University of Kansas Medical Center

Kansas City, Kansas, United States

Local Institution - 0039

New Orleans, Louisiana, United States

Local Institution - 0005

Boston, Massachusetts, United States

Washington University School of Medicine

St Louis, Missouri, United States

Hackensack University Medical Center

Hackensack, New Jersey, United States

Icahn School of Medicine at Mount Sinai

New York, New York, United States

Neurological Institute of New York

New York, New York, United States

University of Cincinnati Medical Center

Cincinnati, Ohio, United States

Cleveland Clinic Mellen Center

Cleveland, Ohio, United States

Oregon Health and Science University

Portland, Oregon, United States

Swedish Medical Center

Seattle, Washington, United States

Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Antwerp University Hospital

Edegem, Antwerpen, Belgium

UZ Gent

Ghent, Oost-Vlaanderen, Belgium

Hopital Claude Huriez - CHU de Lille

Lille, Nord, France

Pitie Salpetriere University Hospital

Paris, Ville de Paris, France

Universitaetsklinikum Essen

Essen, North Rhine-Westphalia, Germany

Universitaetsklinikum Magdeburg

Magdeburg, Saxony-Anhalt, Germany

Local Institution - 0033

Düsseldorf, Germany

Universitaetsklinikum Erlangen

Erlangen, Germany

Klinikum der Universität München Großhadern

München, Germany

Hospital Universitari Vall d'Hebron

Barcelona, Barcelona [Barcelona], Spain

Local Institution - 0016

Barcelona, Barcelona [Barcelona], Spain

Hospital Clínic de Barcelona

Barcelona, Catalunya [Cataluña], Spain

Hospital Universitario Ramón y Cajal

Madrid, Madrid, Comunidad de, Spain

Hospital Universitari i Politecnic La Fe

Valencia, Spain

Manchester Royal Infirmary

Manchester, Lancashire, United Kingdom

University College London Hospital

London, London, City of, United Kingdom

Salford Royal Hospital

Salford, Manchester, United Kingdom

Barts Health NHS Trust

London, United Kingdom

View Full Details on ClinicalTrials.gov

For the most up-to-date information, visit the official listing.

Visit

NCT06220201


Related Trials