RecruitingPhase 3NCT06578247

Quizartinib or Placebo Plus Chemotherapy in Newly Diagnosed Patients With FLT3-ITD Negative AML

A Phase 3, Double-Blind, Randomized, Placebo-Controlled Trial Of Quizartinib Administered in Combination With Induction and Consolidation Chemotherapy and Administered as Maintenance Therapy in Adult Patients With Newly Diagnosed FLT3-ITD Negative Acute Myeloid Leukemia


Sponsor

Daiichi Sankyo

Enrollment

700 participants

Start Date

Nov 19, 2024

Study Type

INTERVENTIONAL

Conditions

Summary

This study will compare the effects of Quizartinib versus placebo in combination with chemotherapy in participants with newly diagnosed FMS-like tyrosine kinase 3 (FLT3)-internal tandem duplication (ITD) negative acute myeloid leukemia (AML).


Eligibility

Min Age: 18 YearsMax Age: 70 Years

Inclusion Criteria5

  • Must be competent and able to comprehend, sign, and date an Ethics Committee (EC)- or Institutional Review Board (IRB)-approved ICF before performance of any trial-specific procedures or tests.
  • ≥18 years or the minimum legal adult age (whichever is greater) and ≤70 years (at Screening).
  • Newly diagnosed, morphologically documented primary AML based on the World Health Organization (WHO) 2016 classification (at Screening)
  • Eastern Cooperative Oncology Group (ECOG) performance status (at the time the participant signs their ICF) of 0-2.
  • Participant is a candidate for standard "7+3" induction chemotherapy regimen as specified in the protocol per investigator assessment

Exclusion Criteria9

  • Diagnosis of acute promyelocytic leukemia (APL), French-American-British classification M3 or WHO classification of APL with translocation, t(15;17)(q22;q12), or BCR-ABL positive leukemia (ie, chronic myelogenous leukemia in blast crisis); participants who undergo diagnostic workup for APL and treatment with all-trans retinoic acid (ATRA), but who are found not to have APL, are eligible (treatment with ATRA must be discontinued before starting induction chemotherapy).
  • Diagnosis of AML secondary to prior chemotherapy or radiotherapy.
  • Diagnosis of AML with known antecedent myelodysplastic syndrome (MDS) or a myeloproliferative neoplasm (MPN) or MDS/MPNs including chronic myelomonocytic leukemia (CMML), atypical chronic myeloid leukemia (aCML), juvenile myelomonocytic leukemia (JMML) and others.
  • Participants with newly diagnosed AML with FLT3-ITD mutations (FLT3-ITD \[+\]) present at ≥5% VAF (or ≥0.05 SR) based on a validated FLT3 mutation assay.
  • Prior treatment for AML, except for the following allowances prior to Day 1 of chemotherapy:
  • Leukapheresis;
  • Treatment for hyperleukocytosis with hydroxyurea;
  • Cranial radiotherapy for central nervous system (CNS) leukostasis;
  • Prophylactic intrathecal chemotherapy

Interventions

DRUGQuizartinib

Participants will receive quizartinib at 60 mg/day orally once daily

DRUGPlacebo

Participants will receive placebo at 60 mg/day orally once daily

DRUGChemotherapy

Participants will receive commercially available cytarabine (cytosine arabinoside) and anthracycline (daunorubicin or idarubicin).


Locations(292)

City of Hope Phoenix

Goodyear, Arizona, United States

Mayo Clinic - Phoenix

Phoenix, Arizona, United States

University of Arizona Cancer Center

Tucson, Arizona, United States

David Geffen School of Medicine

Los Angeles, California, United States

University of California Davis Health System

Sacramento, California, United States

Ucsf - School of Medicine

San Francisco, California, United States

Stanford University School of Medicine- Parent

Stanford, California, United States

Colorado Blood Cancer Institute

Denver, Colorado, United States

Yale University

New Haven, Connecticut, United States

Mayo Clinic Hospital

Jacksonville, Florida, United States

Florida Hospital Cancer Institute - Kissimmee

Kissimmee, Florida, United States

Tampa General Hospital

Tampa, Florida, United States

Moffitt Cancer Center

Tampa, Florida, United States

Winship Cancer Institute of Emory University

Atlanta, Georgia, United States

Augusta University

Augusta, Georgia, United States

Robert H Lurie Comprehensive Cancer Center Northwestern University

Chicago, Illinois, United States

University of Illinois Hospital & Health Sciences System

Chicago, Illinois, United States

The University of Chicago Medical Center

Chicago, Illinois, United States

University of Kentucky

Lexington, Kentucky, United States

Ochsner Medical Center - New Orleans

New Orleans, Louisiana, United States

Johns Hopkins Hospital

Baltimore, Maryland, United States

Massachusetts General Hospital

Boston, Massachusetts, United States

University of Michigan Comprehensive Cancer Center Michigan Medicine

Ann Arbor, Michigan, United States

Henry Ford Hospital

Detroit, Michigan, United States

University of Minnesota Medical School - Twin Cities Campus

Minneapolis, Minnesota, United States

Mayo Clinic

Rochester, Minnesota, United States

Mayo Clinic

Rochester, Minnesota, United States

Washington University

St Louis, Missouri, United States

Hackensack University Medical Center

Hackensack, New Jersey, United States

Thomas Jefferson Univ Hosp

Haddonfield, New Jersey, United States

Roswell Park Comprehensive Cancer Center

Buffalo, New York, United States

Memorial Sloan Kettering Cancer Center - Main

Long Island City, New York, United States

Memorial Sloan Kettering Cancer Center - Main

New York, New York, United States

Upstate University Hospital

Syracuse, New York, United States

University of North Carolina Hospitals

Chapel Hill, North Carolina, United States

Duke Cancer Institute - Sarcoma Research

Durham, North Carolina, United States

University of Cincinnati

Cincinnati, Ohio, United States

Cleveland Clinic Taussig Cancer Center

Cleveland, Ohio, United States

The James Cancer Hospital and Solove Research Institute

Columbus, Ohio, United States

Ohio Health Marion Area Physicians

Columbus, Ohio, United States

Peggy & Charles Stephenson Oklahoma Cancer Ctr

Oklahoma City, Oklahoma, United States

Oregon Health & Science University (Ohsu)

Portland, Oregon, United States

University of Pennsylvania

Philadelphia, Pennsylvania, United States

Upmc Hillman Cancer Center

Pittsburgh, Pennsylvania, United States

Rhode Island Hospital

Providence, Rhode Island, United States

Tristar Bone Marrow Transplant

Nashville, Tennessee, United States

South Austin Medical Center

Austin, Texas, United States

Houston Methodist Hospital

Houston, Texas, United States

The University of Texas Md Anderson Cancer Center

Houston, Texas, United States

Uva Health System

Charlottesville, Virginia, United States

Virginia Commonwealth University (Vcu) Massey Cancer Center

Richmond, Virginia, United States

Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Royal Adelaide Hospital

Adelaide, Australia

Flinders Medical Centre (Fmc)

Bedford Park, Australia

Flinders Medical Centre (Fmc)

Bedford Park, Australia

Box Hill Hospital

Box Hill, Australia

Concord Repatriation General Hospital

Concord, Australia

St Vincent'S Hospital Melbourne

Darlinghurst, Australia

Townsville University Hospital

Douglas, Australia

Liverpool Hospital

Liverpool, Australia

The Alfred Hospital

Melbourne, Australia

Fiona Stanley Hospital

Murdoch, Australia

Sir Charles Gairdner Hospital

Perth, Australia

Princess Alexandra Hospital

Woolloongabba, Australia

Ordensklinikum Linz Gmbh - Elisabethinen

Linz, Austria

LKH - Universitätsklinikum der PMU Salzburg

Salzburg, Austria

Hanusch Krankenhaus Der Wgkk Wien

Vienna, Austria

Institut Jules Bordet

Anderlecht, Belgium

ZNA

Antwerp, Belgium

Az Sint-Jan

Bruges, Belgium

Uz Leuven

Leuven, Belgium

Chu of Liège

Liège, Belgium

AZ DELTA

Roeselare, Belgium

Cetus Hospital Dia Oncologia

Belo Horizonte, Brazil

Unesp - Faculdade de Medicina Da Universidade Estadual Paulista - Campus Botucatu

Botucatu, Brazil

Centro de Hematologia E Hemoterapia - Hemocentro de Campinas - Unicamp

Campinas, Brazil

Centro de Hematologia e Hemoterapia - Hemocentro de Campinas - UNICAMP

Campinas, Brazil

Hospital Erasto Gaertner - Liga Paranaense de Combate ao Câncer

Curitiba, Brazil

Hospital Erasto Gaertner - Liga Paranaense de Combate Ao Că'Ncer

Curitiba, Brazil

Cepon - Centro De Pesquisas Oncolagicas de Santa Catarina

Florianópolis, Brazil

HUWC - UFC - Hospital Universitário Walter Cantídio - Universidade Federal do Ceará

Fortaleza, Brazil

HC-UFG - Hospital das Clínicas da Universidade Federal de Goiás

Goiânia, Brazil

Hc-Ufg - Hospital Das Clă Nicas Da Universidade Federal de Goiă S

Goiânia, Brazil

Fundacao Doutor Amaral Carvalho

Jaú, Brazil

Fundaã§Ã£O Doutor Amaral Carvalho

Jaú, Brazil

Hospital de Clínicas de Passo Fundo

Passo Fundo, Brazil

Hospital de Clă Nicas de Passo Fundo

Passo Fundo, Brazil

Santa Casa de Misericórdia de Porto Alegre

Porto Alegre, Brazil

Hospital de Clă Nicas de Porto Alegre

Porto Alegre, Brazil

Hospital Ernesto Dornelles

Porto Alegre, Brazil

INCA - Instituto Nacional de Cancer

Rio de Janeiro, Brazil

Fundacao Faculdade Regional de Medicina de Sao Jose Do Rio Preto

Sao Jose Rio Preto, Brazil

ICESP - Instituto do Câncer do Estado de São Paulo Octavio Frias de Oliveira

São Paulo, Brazil

Hospital Beneficencia Portuguesa da Sao Paulo

São Paulo, Brazil

Hospital Nove de Julho

São Paulo, Brazil

Sírio-Libanês Brasilia-Centro de Oncologia-Asa Sul

São Paulo, Brazil

Icesp - Instituto Do Câncer Do Estado de São Paulo Octavio Frias de Oliveira

SĂŁo Paulo, Brazil

Umhat 'Dr. Georgi Stranski', Ead

Pleven, Bulgaria

Umhat 'Sv. Georgi', Ead

Plovdiv, Bulgaria

Umhat  Sv. Ivan Rilskiâ , Ead

Sofia, Bulgaria

Military Medical Academy - Mhat - Sofia

Sofia, Bulgaria

'Shathd' Ead Sofia

Sofia, Bulgaria

Umhat Prof. Dr. Stoyan Kirkovich Ad

Stara Zagora, Bulgaria

London Health Sciences Centre

London, Canada

McGill University - Dept. Oncology Clinical Research Program

Montreal, Canada

The Ottawa Hospital - General Campus

Ottawa, Canada

Saskatoon Cancer Centre

Saskatoon, Canada

Princess Margaret Cancer Center

Toronto, Canada

Peking University First Hospital

Beijing, China

Peking University Third Hospital

Beijing, China

Peking Union Medical College Hospital

Beijing, China

The First Hospital of Jilin University

Changchun, China

Xiangya Hospital, Central South University

Changsha, China

The Second Xiangya Hospital of Central South University

Changsha, China

The First Affiliated Hospital of Chongqing Medical University

Chongqing, China

Sun Yat-Sen University, Cancer Center

Guangzhou, China

Guangdong Provincial People'S Hospital

Guangzhou, China

Guangdong Provincial People's Hospital

Guangzhou, China

Qilu Hospital of Shandong University

Jinan, China

The First Affiliated Hospital of Nanchang University

Nanchang, China

Zhong Da Hospital, Southeast University

Nanjing, China

Affiliated Hospital of Nantong University

Nantong, China

The Affiliated Hospital of Qingdao University

Qingdao, China

Shanghai Tongren Hospital

Shanghai, China

Shengjing Hospital of China Medical University

Shengyang, China

Shenzhen Second People'S Hospital

Shenzhen, China

The Second Hospital of Hebei Medicical University

Shijiazhuang, China

The First Affiliated Hospital of Soochow University

Suzhou, China

Institute of Hematology and Hospital of Blood Disease

Tianjin, China

Tianjin Medical University General Hospital

Tianjin, China

The First Affiliated Hospital of Wenzhou Medical University

Wenzhou, China

Wuxi People'S Hospital

Wuxi, China

The First Affiliated Hospital of Xiâ An Jiaotong University

Xi'an, China

Yantai Yuhuangding Hospital

Yantai, China

Henan Cancer Hospital

Zhengzhou, China

Clinical Hospital Centre Rijeka

Rijeka, Croatia

Clinical Hospital Centar Zagreb

Zagreb, Croatia

Clinical Hospital Dubrava

Zagreb, Croatia

Fakultni Nemocnice Brno

Brno, Czechia

Fakultni Nemocnice Hradec Kralove

Hradec Králové, Czechia

Fakultni Nemocnice Plzen

Pilsen, Czechia

Fakultni Nemocnice Ostrava

Poruba, Czechia

Fakultni Nemocnice Kralovske Vinohrady

Prague, Czechia

Ustav Hematologie A Krevni Transfuze

Prague, Czechia

Chu Angers - Hă"Pital Hă"Tel Dieu

Angers, France

Chu de Caen

Caen, France

Chu de Grenoble - Hospital Albert Michallon

La Tronche, France

Centre Hospitalier de Versailles

Le Chesnay, France

Hopital Claude Huriez - Chru Lille

Lille, France

Centre Léon Bérard

Lyon, France

Hopital de La Conception - Aphm

Marseille, France

Chu de Nantes - Hotel Dieu

Nantes, France

CHU Nice - Hôpital de l'Archet 1

Nice, France

Hospital Saint-Louis

Paris, France

Chu de Bordeaux - Hă"Pital Haut-Lă Vă Que

Pessac, France

Centre Hospitalier Lyon Sud

Pierre BĂŠnite, France

Chu Rennes - Hopital Pontchaillou

Rennes, France

Chu Amiens - Hopital Sud

Salouël, France

Institut de Cancă Rologie de Strasbourg Europe - Icans

Strasbourg, France

Institut Universitaire Du Cancer de Toulouse- Iuct-O

Toulouse, France

Institut Gustave Roussy

Villejuif, France

Klinikum Aschaffenburg-Alzenau

Alzenau in Unterfranken, Germany

Charité Campus Virchow-Klinikum

Berlin, Germany

Staedtisches Klinikum Braunschweig Ggmbh

Braunschweig, Germany

Universitaetsklinikum Carl Gustav Carus Tu Dresden

Dresden, Germany

Universitaetsklinikum Essen

Essen, Germany

Krh Klinikum Siloah

Hanover, Germany

Universitaetsklinikum Heidelberg

Heidelberg, Germany

Universitaetsklinikum Heidelberg

Heidelberg, Germany

Universitaetsklinikum Schleswig-Holstein

Kiel, Germany

Universită"Tsklinikum Leipzig Klinik Fă R Hă"Matologie Internistische Onkologie Hă"Mostaseol

Leipzig, Germany

Universitaetsklinikum Muenster

Münster, Germany

Universitaetsklinikum Muenster

Münster, Germany

The University of Hong Kong

Hong Kong, Hong Kong

The Chinese University of Hong Kong (Cuhk)

Shatin, Hong Kong

Semmelweis Egyetem

Budapest, Hungary

Debreceni Egyetem

Debrecen, Hungary

Gyor-Moson-Sopron Varmegyei Petz Aladar Egyetemi Oktato Korhaz

Győr, Hungary

Szegedi Tudomanyegyetem Szent-Gyorgyi Albert Klinikai Kozpont

Szeged, Hungary

Azienda Ospedaliero Universitaria Consorziale Policlinico Di Bari

Bari, Italy

Azienda Socio Sanitaria Territoriale Degli Spedali Civili Di Brescia (Presidio Spedali Civili)

Brescia, Italy

Irccs Istituto Scientifico Romagnolo Per Lo Studio Dei Tumori 'Dino Amadori' - Irst

Meldola, Italy

Ospedale San Raffaele

Milan, Italy

Azienda Socio Sanitaria Territoriale Niguarda (Grande Ospedale Metropolitano Niguarda)

Milan, Italy

Ospedale Maggiore Di Novara

Novara, Italy

Azienda Ospedaliera Vincenzo Cervello

Palermo, Italy

Fondazione Policlinico Universitario Agostino Gemelli Irccs

Roma, Italy

Azienda Ospedaliera Universitaria Policlinico Tor Vergata

Rome, Italy

Azienda Ospedaliera Universitaria Policlinico Tor Vergata

Rome, Italy

Istituto Clinico Humanitas

Rozzano, Italy

Irccs Ospedale Casa Sollievo Della Sofferenza

San Giovanni Rotondo, Italy

Azienda Ospedaliero-Universitaria Cittă Della Salute E Della Scienza Di Torino

Torino, Italy

Ospedale Mauriziano Umberto I

Torino, Italy

Asst Dei Sette Laghi Ospedale Di Circolo E Fondazione Macchi Varese

Varese, Italy

Akita University Hospital

Akita, Japan

Aomori Prefetural Central Hospital

Aomori, Japan

Tokyo Metropolitan Cancer and Infectious Diseases Center Komagome Hospital

Bunkyō City, Japan

Chiba Aoba Municipal Hospital

Chiba, Japan

Kyushu University Hospital

Fukuoka, Japan

Chugoku Central Hospital

Fukuyama, Japan

Gifu Municipal Hospital

Gifu, Japan

Hamamatsu University School of Medicine, University Hospital

Hamamatsu, Japan

Tesshokai Kameda General Hospital

Kamogawa-shi, Japan

Kanazawa University Hospital

Kanazawa, Japan

National Hospital Organization Kumamoto Medical Center

Kumamoto, Japan

Saiseikai Maebashi Hospital

Maebashi, Japan

Ehime Prefectural Central Hospital

Matsuyama, Japan

Nagoya University Hospital

Nagoya, Japan

Japan RED CROSS OSAKA HOSPITAL

Osakar, Japan

Hokkaido University Hospital

Sapporo, Japan

Sapporo Hokuyu Hospital

Sapporo, Japan

Tenri Hospital

Tenri, Japan

Haukeland Universitetssykehus

Bergen, Norway

Oslo University Hospital

Oslo, Norway

University Hospital of North Norway

Tromsø, Norway

Klinika Hematoonkologii I Transplantacji Szpiku

Lublin, Poland

Spzoz Msw Zwarmiĺsko-Mazurskimcen.Onko.Wolsztynie

Olsztyn, Poland

Wojewodzki Szpital Zespolony Im. L. Rydygiera W Toruniu

Torun, Poland

Instytut Hematologii I Transfuzjologii

Warsaw, Poland

Centro Hospitalar de Lisboa Norte, E.P.E. - Hospital de Santa Maria

Lisbon, Portugal

Instituto Portugues De Oncologia do Porto Francisco Gentil, EPE

Porto, Portugal

Spitalul Clinic Colentina

Bucharest, Romania

Institutul Clinic Fundeni

Bucharest, Romania

Spitalul Clinic Coltea

Bucharest, Romania

Institutul Oncologic Prof. Dr. Ion Chiricuta Cluj-Napoca

Cluj-Napoca, Romania

Spitalul Clinic Municipal Filantropia Craiova

Craiova, Romania

Military Medical Academy

Belgrade, Serbia

University Clinical Center of Serbia

Belgrade, Serbia

University Clinical Center Nis

Niš, Serbia

National University Hospital

Singapore, Singapore

Curie Oncology Pte Ltd

Singapore, Singapore

Inje University Haeundae Paik Hospital

Busan, South Korea

Pusan National University Hospital

Busan, South Korea

Kyungpook National University Chilgok Hospital

Daegu, South Korea

Yeungnam University Hospital

Daegu, South Korea

Daegu Catholic University Medical Center

Daegu, South Korea

Chonnam National University Hwasun Hospital

Hwasun-gun, South Korea

Gachon University Gil Medical Center

Incheon, South Korea

Jeonbuk National University Hospital

Jeonju, South Korea

Seoul National University Bundang Hospital

Seongnam-si, South Korea

Severance Hospital, Yonsei University Health System

Seoul, South Korea

Samsung Medical Center

Seoul, South Korea

The Catholic University of Korea, Seoul St. Mary'S Hospital

Seoul, South Korea

Korea University Guro Hospital

Seoul, South Korea

Seoul National University Hospital

Seoul, South Korea

Asan Medical Center

Seoul, South Korea

Ajou University Hospital

Suwon, South Korea

Ulsan University Hospital

Ulsan, South Korea

Complejo Hospitalario Universitario de Albacete

Albacete, Spain

Ico Badalona - Hospital Universitari Germans Trias I Pujol

Badalona, Spain

Hospital de La Santa Creu I Sant Pau

Barcelona, Spain

Hospital Universitari Vall D'Hebron

Barcelona, Spain

Hospital Universitario De Burgos

Burgos, Spain

Hospital San Pedro de Alcantara

Cáceres, Spain

Hospital Universitario Reina Sofia

Córdoba, Spain

Hospital Universitario de Gran Canaria Dr. Negrin

Las Palmas, Spain

Clinica Universidad de Navarra

Madrid, Spain

Md Anderson Cancer Centre

Madrid, Spain

Hospital Universitario Fundacion Jimenez Diaz

Madrid, Spain

Hospital Universitario 12 de Octubre

Madrid, Spain

Hospital Universitario La Paz

Madrid, Spain

Hospital Universitario Puerta de Hierro Majadahonda

Majadahonda, Spain

Hospital Regional Universitario de Malaga

Málaga, Spain

Hospital General Universitario Morales Meseguer

Murcia, Spain

Hospital Universitari Son Espases

Palma de Mallorca, Spain

Hospital Universitario Quironsalud Madrid

Pozuelo de Alarcón, Spain

Hospital Clinico Universitario de Salamanca

Salamanca, Spain

Hospital Universitario Marques de Valdecilla

Santander, Spain

Complejo Hospitalario Universitario de Santiago

Santiago de Compostela, Spain

Hospital Universitario Virgen Del Rocio

Seville, Spain

Hospital Clinico Universitario de Valencia

Valencia, Spain

Hospital Universitario Dr. Peset

Valencia, Spain

Hospital Universitari I Politecnic La Fe

Valencia, Spain

Sahlgrenska Universitetssjukhuset

Gasteborg, Sweden

Skă Nes Universitetssjukhus, Lund

Lund, Sweden

Akademiska Sjukhuset

Uppsala, Sweden

Inselspital - Universitaetsspital Bern

Bern, Switzerland

Inselspital - Universitaetsspital Bern

Bern, Switzerland

Luzerner Kantonsspital - Luzern

Lazern 16, Switzerland

Kaohsiung Chang Gung Memorial Hospital

Kaohsiung City, Taiwan

China Medical University Hospital

Taichung, Taiwan

National Cheng Kung University Hospitalx

Tainan, Taiwan

National Taiwan University Hospital

Taipei, Taiwan

Taipei Veterans General Hospital

Taipei, Taiwan

Chang Gung Memorial Hospital

Taoyuan, Taiwan

Queen Elizabeth Hospital

Birmingham, United Kingdom

King'S College Hospital

London, United Kingdom

Hammersmith Hospital

London, United Kingdom

Maidstone Hospital

Maidstone, United Kingdom

Manchester Royal Infirmary

Manchester, United Kingdom

Churchill Hospital

Oxford, United Kingdom

Torbay Hospital

Torquay, United Kingdom

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NCT06578247


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