RecruitingNCT06805695
Long-term Follow-up (LTFU) Study of Participants in Any iECURE Protocol Using an Investigational Product (IP)
Sponsor
iECURE, Inc.
Enrollment
13 participants
Start Date
Dec 23, 2024
Study Type
OBSERVATIONAL
Conditions
Summary
This LTFU is being conducted to assess long-term safety and durability of response in participants dosed with IP in a parent protocol, and to collect longitudinal natural history in enrolled but not dosed participants who also participated in a parent protocol.
Eligibility
Min Age: 7 MonthsMax Age: 15 Months
Inclusion Criteria3
- Enrolled in an iECURE parent protocol and have either completed or discontinued that protocol
- Participant parent(s)/LAR is willing and able to adhere to the protocol requirements.
- Consent was obtained by the participants parent(s)/LAR (and participant assent, where applicable), prior to any study-related data being collected.
Exclusion Criteria1
- \. Participants who enroll into an interventional drug or gene therapy clinical trial utilizing an IP other than the IP provided in the parent protocol will be excluded from this protocol.
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Interventions
OTHERNo Intervention
No Intervention
Locations(1)
View Full Details on ClinicalTrials.gov
For the most up-to-date information, visit the official listing.
NCT06805695
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