RecruitingPhase 3NCT07482176

Efficacy and Safety Study of Ixoberogene Soroparvovec (Ixo-vec) in Participants With Neovascular Age-related Macular Degeneration (AQUARIUS)

A Multi-center, Randomized, Double-masked, Active-comparator-controlled, Phase 3 Study to Evaluate the Efficacy and Safety of Ixoberogene Soroparvovec (Ixo-vec) in Participants With Neovascular Age-related Macular Degeneration (AQUARIUS)


Sponsor

Adverum Biotechnologies, Inc.

Enrollment

284 participants

Start Date

Mar 16, 2026

Study Type

INTERVENTIONAL

Conditions

Summary

This is a multi-center, randomized, double-masked, active-comparator-controlled, Phase 3 study in a broad participant population (treatment-naïve and treatment-experienced) with neovascular (wet) age-related macular degeneration (nAMD). The study will evaluate a single intravitreal (IVT) injection of Ixo-vec compared to intravitreal aflibercept (active comparator). The primary endpoint of this study is the mean change in best corrected visual acuity (BCVA) of Ixo-vec compared to an active comparator measured as an average at Weeks 52 and 56. Safety, tolerability, and efficacy will be evaluated throughout the study.


Eligibility

Min Age: 50 Years

Plain Language Summary

Simplified for easier understanding

This clinical trial is studying a drug called Aflibercept and Ixo-vec for people with neovascular age-related macular degeneration (namd) and wet amd. The study is currently recruiting participants at 79 locations.

This summary was AI-generated to explain the trial in plain language. It is not medical advice. Always discuss eligibility with your doctor before enrolling in a clinical trial.

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Interventions

GENETICIxo-vec

Ixo-vec will be administered intravitreally.

DRUGAflibercept

Aflibercept will be administered intravitreally.


Locations(79)

Adverum Clinical Site 245

Mesa, Arizona, United States

Adverum Clinical Site 126

Phoenix, Arizona, United States

Adverum Clinical Site 178

Phoenix, Arizona, United States

Adverum Clinical Site 223

Phoenix, Arizona, United States

Adverum Clinical Site 229

Scottsdale, Arizona, United States

Adverum Clinical Site 242

Sun City, Arizona, United States

Adverum Clinical Site 198

Springdale, Arkansas, United States

Adverum Clinical Site 109

Bakersfield, California, United States

Adverum Clinical Site 100

Beverly Hills, California, United States

Adverum Clinical Site 201

Campbell, California, United States

Adverum Clinical Site 172

Encino, California, United States

Adverum Clinical Site 169

Fullerton, California, United States

Adverum Clinical Site 224

Huntington Beach, California, United States

Adverum Clinical Site 130

Poway, California, United States

Adverum Clinical Site 215

Redlands, California, United States

Adverum Clinical Site 140

Sacramento, California, United States

Adverum Clinical Site 212

Sacramento, California, United States

Adverum Clinical Site 175

Santa Barbara, California, United States

Adverum Clinical Site 202

Torrance, California, United States

Adverum Clinical Site 189

Walnut Creek, California, United States

Adverum Clinical Site 200

Denver, Colorado, United States

Adverum Clinical Site 116

Denver, Colorado, United States

Adverum Clinical Site 165

Waterford, Connecticut, United States

Adverum Clinical Site 124

Deerfield Beach, Florida, United States

Adverum Clinical Site 184

Deerfield Beach, Florida, United States

Adverum Clinical Site 176

Fort Lauderdale, Florida, United States

Adverum Clinical Site 221

Fort Myers, Florida, United States

Adverum Clinical Site 236

Gainesville, Florida, United States

Adverum Clinical Site 214

Lakeland, Florida, United States

Adverum Clinical Site 168

Miami Springs, Florida, United States

Adverum Clinical Site 213

Orlando, Florida, United States

Adverum Clinical Site 206

Plantation, Florida, United States

Adverum Clinical Site 183

South Miami, Florida, United States

Adverum Clinical Site 120

St. Petersburg, Florida, United States

Adverum Clinical Site 148

Tampa, Florida, United States

Adverum Clinical Site 238

Winter Haven, Florida, United States

Adverum Clinical Site 182

Augusta, Georgia, United States

Adverum Clinical Site 246

Chicago, Illinois, United States

Adverum Clinical Site 179

Oak Forest, Illinois, United States

Adverum Clinical Site 207

Oak Park, Illinois, United States

Adverum Clinical Site 195

Carmel, Indiana, United States

Adverum Clinical Site 205

Carmel, Indiana, United States

Adverum Clinical Site 253

Carmel, Indiana, United States

Adverum Clinical Site 197

Hagerstown, Maryland, United States

Adverum Clinical Site 204

Hagerstown, Maryland, United States

Adverum Clinical Site 216

Jackson, Mississippi, United States

Adverum Clinical Site 240

Bloomfield, New Jersey, United States

Adverum Clinical Site 171

Teaneck, New Jersey, United States

Adverum Clinical Site 225

Liverpool, New York, United States

Adverum Clinical Site 244

Rochester, New York, United States

Adverum Clinical Site 196

Asheville, North Carolina, United States

Adverum Clinical Site 234

Cary, North Carolina, United States

Adverum Clinical Site 211

Greensboro, North Carolina, United States

Adverum Clinical Site 219

Greensboro, North Carolina, United States

Adverum Clinical Site 220

Hickory, North Carolina, United States

Adverum Clinical Site 209

Wake Forest, North Carolina, United States

Adverum Clinical Site 248

Beachwood, Ohio, United States

Adverum Clinical Site 247

Cleveland, Ohio, United States

Adverum Clinical Site 254

Edmond, Oklahoma, United States

Adverum Clinical Site 252

Portland, Oregon, United States

Adverum Clinical Site 181

Erie, Pennsylvania, United States

Adverum Clinical Site 239

Philadelphia, Pennsylvania, United States

Adverum Clinical Site 110

Philadelphia, Pennsylvania, United States

Adverum Clinical Site 241

Bluffton, South Carolina, United States

Adverum Clinical Site 222

Ladson, South Carolina, United States

Adverum Clinical Site 101

Nashville, Tennessee, United States

Adverum Clinical Site 145

Arlington, Texas, United States

Adverum Clinical Site 127

Austin, Texas, United States

Adverum Clinical Site 243

Austin, Texas, United States

Adverum Clinical Site 107

Conroe, Texas, United States

Adverum Clinical Site 194

Dallas, Texas, United States

Adverum Clinical Site 162

McAllen, Texas, United States

Adverum Clinical Site 185

San Antonio, Texas, United States

Adverum Clinical Site 232

San Marcos, Texas, United States

Adverum Clinical Site 228

Schertz, Texas, United States

Adverum Clinical Site 231

The Woodlands, Texas, United States

Adverum Clinical Site 237

Tyler, Texas, United States

Adverum Clinical Site 199

Lynchburg, Virginia, United States

Adverum Clinical Site 249

Silverdale, Washington, United States

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NCT07482176


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