AMI Clinical Trials in Boston, Massachusetts

23 recruitingBoston, Massachusetts

Showing 120 of 23 trials

Recruiting
Phase 2

A Study of Lower Radiotherapy Dose to Treat Children With CNS Germinoma

GerminomaBasal Ganglia GerminomaDiabetes Insipidus+3 more
Children's Oncology Group240 enrolled109 locationsNCT06368817
Recruiting
Phase 3

A Study to Test Whether Nerandomilast Can Help Slow Down Changes in the Lung in People With a Family History of Pulmonary Fibrosis

Interstitial Lung DiseasesFamilial Pulmonary FibrosisInterstitial Lung Abnormalities
Boehringer Ingelheim80 enrolled56 locationsNCT07201922
Recruiting
Phase 1

A Study of SGT-501 Gene Therapy in Catecholaminergic Polymorphic Ventricular Tachycardia (CPVT)

Catecholaminergic Polymorphic Ventricular Tachycardia
Solid Biosciences Inc.18 enrolled5 locationsNCT07148089
Recruiting

International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registry

Gaucher DiseaseCerebroside Lipidosis SyndromeGlucocerebrosidase Deficiency Disease+1 more
Genzyme, a Sanofi Company12,000 enrolled318 locationsNCT00358943
Recruiting
Not Applicable

Effect of CPAP on 6-Minute Walk Test Outcomes in Patients With ECAC

TracheobronchomalaciaExcessive Dynamic Airway Collapse
Beth Israel Deaconess Medical Center32 enrolled1 locationNCT04217603
Recruiting
Not Applicable

Patients and Families Improving Safety in Hospitals by Actively Reporting Experiences

Health DisparitiesPatient SafetyQuality Improvement+3 more
Boston Children's Hospital656 enrolled1 locationNCT05407129
Recruiting
Phase 1

The ENERGY Study: Evaluation of Safety and Tolerability of INZ-701 in Infants With ENPP1 Deficiency or ABCC6 Deficiency

Pseudoxanthoma ElasticumEctonucleotide Pyrophosphatase/phosphodiesterase1 DeficiencyAutosomal Recessive Hypophosphatemic Rickets+2 more
Inozyme Pharma16 enrolled7 locationsNCT05734196
Recruiting
Phase 3

Phase 3 Trial of eRapa in Patients With Familial Adenomatous Polyposis

Familial Adenomatous Polyposis (FAP)
Rapamycin Holdings Inc.168 enrolled26 locationsNCT06950385
Recruiting
Phase 1

Nucleoside Therapy in Patients With Telomere Biology Disorders

Dyskeratosis CongenitaTelomere Biology DisordersHoyeraal-Hreidarsson Syndrome+4 more
Suneet Agarwal36 enrolled1 locationNCT06817590
Recruiting
Phase 3

A Trial of Setmelanotide in Patients With Congenital Hypothalamic Obesity (Sub-study of NCT05774756)

Hypothalamic ObesityMultiple Pituitary Hormone Deficiency Genetic FormSepto-Optic Dysplasia+3 more
Rhythm Pharmaceuticals, Inc.39 enrolled11 locationsNCT06760546
Recruiting
Phase 3

Open-label Extension Study to Evaluate Metreleptin in Patients With Partial Lipodystrophy

Familial Partial Lipodystrophy
Amryt Pharma24 enrolled7 locationsNCT06679270
Recruiting
Phase 2

Kisspeptin Administration Subcutaneously to Patients With Hypothalamic Amenorrhea

Hypogonadotropic HypogonadismHypothalamic Amenorrhea
Stephanie B. Seminara, MD20 enrolled1 locationNCT07224438
Recruiting
Phase 1Phase 2

A Study of RM-718 in Healthy Subjects and Patients With MC4R Pathway Impairment

Prader-Willi SyndromeHypothalamic ObesityPWS
Rhythm Pharmaceuticals, Inc.150 enrolled7 locationsNCT06239116
Recruiting

PROPEL - A Prospective Observational Patient Registry to Evaluate ENPP1 and ABCC6 Deficiency

ATP-Binding Cassette Subfamily C Member 6 DeficiencyEctonucleotide Pyrophosphatase/Phosphodiesterase 1 Deficiency
Inozyme Pharma1,000 enrolled14 locationsNCT06302439
Recruiting
Not Applicable

Computerized Decision Support for Identification and Management of Familial Hypercholesterolemia

Familial Hypercholesterolaemia
Brigham and Women's Hospital450 enrolled1 locationNCT06743659
Recruiting

International Rare Histiocytic Disorders Registry (IRHDR)

Rare Histiocytic Disorders (RHDs)Erdheim-Chester Disease (ECD)Rosai-Dorfman Disease (RDD)+7 more
The Hospital for Sick Children400 enrolled15 locationsNCT02285582
Recruiting

Post Marketing Observational Study on Safety of BALFAXAR vs. KCENTRA for Reversal of Vitamin K Antagonist Induced Anticoagulation in Adults Undergoing Urgent Surgery or Invasive Procedure

Vitamin K-Dependent Coagulation DefectSignificant Bleeding Risk
Octapharma3,574 enrolled1 locationNCT06429787
Recruiting

High Dose Interval Vitamin D Supplementation in Patients With Inflammatory Bowel Disease Receiving Biologic Therapy

Crohn DiseaseUlcerative ColitisInflammatory Bowel Disease+1 more
Boston Children's Hospital50 enrolled1 locationNCT04331639
Recruiting
Not Applicable

Gamma Light and Sound Stimulation to Prevent Dementia in Cognitively Normal People At Risk for Alzheimer's Disease

Alzheimer DiseaseFamily Members
Massachusetts General Hospital200 enrolled2 locationsNCT05776641
Recruiting

Longitudinal Study of Urea Cycle Disorders

Brain Diseases, Metabolic, InbornAmino Acid Metabolism, Inborn ErrorsUrea Cycle Disorders
Andrea Gropman1,500 enrolled15 locationsNCT00237315