AMI Clinical Trials in Philadelphia, Pennsylvania

20 recruitingPhiladelphia, Pennsylvania

Showing 120 of 20 trials

Recruiting
Phase 2

A Study of Lower Radiotherapy Dose to Treat Children With CNS Germinoma

GerminomaBasal Ganglia GerminomaDiabetes Insipidus+3 more
Children's Oncology Group240 enrolled109 locationsNCT06368817
Recruiting
Phase 3

A Study to Test Whether Nerandomilast Can Help Slow Down Changes in the Lung in People With a Family History of Pulmonary Fibrosis

Interstitial Lung DiseasesFamilial Pulmonary FibrosisInterstitial Lung Abnormalities
Boehringer Ingelheim80 enrolled56 locationsNCT07201922
Recruiting
Phase 1

A Study of SGT-501 Gene Therapy in Catecholaminergic Polymorphic Ventricular Tachycardia (CPVT)

Catecholaminergic Polymorphic Ventricular Tachycardia
Solid Biosciences Inc.18 enrolled5 locationsNCT07148089
Recruiting
Phase 1Phase 2

Evaluate REC-4881 in Participants With Familial Adenomatous Polyposis (FAP)

Familial Adenomatous Polyposis
Recursion Pharmaceuticals Inc.67 enrolled17 locationsNCT05552755
Recruiting

International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registry

Gaucher DiseaseCerebroside Lipidosis SyndromeGlucocerebrosidase Deficiency Disease+1 more
Genzyme, a Sanofi Company12,000 enrolled318 locationsNCT00358943
Recruiting
Not Applicable

Evaluating Novel Healthcare Approaches to Nurturing and Caring for Hospitalized Elders

Patient SatisfactionAlzheimer DiseaseCaregiver Burden+7 more
University of Michigan1,900 enrolled7 locationsNCT05929703
Recruiting
Phase 1

The ENERGY Study: Evaluation of Safety and Tolerability of INZ-701 in Infants With ENPP1 Deficiency or ABCC6 Deficiency

Pseudoxanthoma ElasticumEctonucleotide Pyrophosphatase/phosphodiesterase1 DeficiencyAutosomal Recessive Hypophosphatemic Rickets+2 more
Inozyme Pharma16 enrolled7 locationsNCT05734196
Recruiting
Phase 3

A Trial of Setmelanotide in Patients With Congenital Hypothalamic Obesity (Sub-study of NCT05774756)

Hypothalamic ObesityMultiple Pituitary Hormone Deficiency Genetic FormSepto-Optic Dysplasia+3 more
Rhythm Pharmaceuticals, Inc.39 enrolled11 locationsNCT06760546
Recruiting
Phase 3

Open-label Extension Study to Evaluate Metreleptin in Patients With Partial Lipodystrophy

Familial Partial Lipodystrophy
Amryt Pharma24 enrolled7 locationsNCT06679270
Recruiting

UPenn Observational Research Repository on Neurodegenerative Disease

Corticobasal Syndrome(CBS)Progressive Supranuclear Palsy (PSP)Primary Progressive Aphasia(PPA)+6 more
University of Pennsylvania1,000 enrolled1 locationNCT04715399
Recruiting

Resuscitative TEE Collaborative Registry

Cardiac ArrestShockHemodynamic Instability+2 more
University of Pennsylvania1,000 enrolled1 locationNCT04972526
Recruiting

PROPEL - A Prospective Observational Patient Registry to Evaluate ENPP1 and ABCC6 Deficiency

ATP-Binding Cassette Subfamily C Member 6 DeficiencyEctonucleotide Pyrophosphatase/Phosphodiesterase 1 Deficiency
Inozyme Pharma1,000 enrolled14 locationsNCT06302439
Recruiting

HoFH, the International Clinical Collaborators Registry

Homozygous Familial Hypercholesterolemia
University of Pennsylvania1,000 enrolled4 locationsNCT04815005
Recruiting
Phase 4

Post-cesarean Analgesia: Comparing Effectiveness of Staggered v. Simultaneous Therapies

cesarean deliveryPost Operative PainPostpartum Comfort+3 more
Thomas Jefferson University825 enrolled1 locationNCT07102641
Recruiting
Not Applicable

Investigation of β-hydroxybutyrate Supplementation as Chemoprevention in Familial Adenomatous Polyposis

Familial Adenomatous PolyposisFAP
Abramson Cancer Center at Penn Medicine20 enrolled1 locationNCT06578637
Recruiting
Phase 2

Efficacy and Safety of Phentermine/Topiramate in Youth With Hypothalamic Obesity

CraniopharyngiomaHypothalamic ObesityHypothalamic Tumor
Seattle Children's Hospital24 enrolled2 locationsNCT06299891
Recruiting

Long-Term SafEty and Clinical Outcomes of LivmArli in Patients in the United States (LEAP-US)

Progressive Familial Intrahepatic CholestasisAlagille Syndrome
Mirum Pharmaceuticals, Inc.70 enrolled8 locationsNCT06193928
Recruiting
Not Applicable

A Post-marketing Study to Evaluate a Novel Surgical Monitoring Technique Using the EARP Nerve Cuff in TLIF Surgery.

Transforaminal Lumbar Interbody Fusion Surgery
Retropsoas Technologies, LLC30 enrolled2 locationsNCT06204900
Recruiting

LOWER: Lomitapide Observational Worldwide Evaluation Registry

Homozygous Familial Hypercholesterolemia
Amryt Pharma300 enrolled75 locationsNCT02135705
Recruiting

Longitudinal Study of Urea Cycle Disorders

Brain Diseases, Metabolic, InbornAmino Acid Metabolism, Inborn ErrorsUrea Cycle Disorders
Andrea Gropman1,500 enrolled15 locationsNCT00237315