Batten Disease Clinical Trials
Batten Disease Trials at a Glance
7 actively recruiting trials for batten disease are listed on ClinicalTrialsFinder across 6 cities in 2 countries. The largest study group is Phase 1 with 1 trial, with the heaviest enrollment activity in Bethesda, Columbia, and Durham. Lead sponsors running batten disease studies include Foundation Fighting Blindness, Joanne Kurtzberg, MD, and Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD).
Browse batten disease trials by phase
Top cities for batten disease trials
Treatments under study
About Batten Disease Clinical Trials
Looking for clinical trials for Batten Disease? There are currently 7 studies actively recruiting participants. Clinical trials offer access to new treatments before they are widely available, and every approved therapy in use today was first tested through a clinical trial.
Below you can browse trials, sign up for alerts when new Batten Disease trials open, and view eligibility criteria for each study. Each listing includes the study phase, locations, and enrollment details.
Frequently Asked Questions
Common questions about Batten Disease clinical trials
A clinical trial is a carefully designed research study that tests new medical treatments, drugs, devices, or approaches in human volunteers. Every approved medication and treatment available today was proven safe and effective through clinical trials.
All clinical trials are reviewed and approved by Institutional Review Boards (IRBs) — independent committees that evaluate patient safety. Trials follow strict protocols, and your health is monitored closely throughout. You can withdraw at any time.
Not necessarily. Many trials compare the new treatment against the current standard of care, meaning all participants receive active treatment. When placebos are used, they are typically combined with standard treatment, not given alone. The trial description will always specify the design.
Under the Affordable Care Act, most private insurers are required to cover routine patient care costs during a clinical trial. The sponsor typically covers the investigational treatment itself. Medicare also covers routine costs for qualifying trials.
Yes. Participation is completely voluntary. You can withdraw at any time, for any reason, without it affecting your access to standard medical care.
Each trial has specific eligibility criteria — including age, diagnosis, disease stage, prior treatments, and general health. Browse the trials listed above and check their eligibility sections. You can also contact the trial site directly to discuss your situation.
Showing 1–7 of 7 trials