Congenital Clinical Trials in Boston, Massachusetts
21 recruitingBoston, Massachusetts
Showing 1–20 of 21 trials
Recruiting
Not Applicable
Starlight Cardiovascular Lifeline Ductus Arteriosus Stent IDE Study
Congenital Heart DiseaseCongenital Heart Disease (CHD)
Starlight Cardiovascular Inc35 enrolled8 locationsNCT07114718
Recruiting
Outcomes and Health Care Resource Utilization in Pediatric Congenital Heart Disease Patients Undergoing Non-Cardiac Procedures
Congenital Heart Disease in Children
Boston Children's Hospital10,000 enrolled10 locationsNCT04604418
Recruiting
Muscle Health Measurements Using Electrical Impedance Myography
Muscular DystrophiesMyositisCongenital Myopathy+4 more
Beth Israel Deaconess Medical Center150 enrolled1 locationNCT07502989
Recruiting
Molecular and Genetic Studies of Congenital Myopathies
Nemaline MyopathyCentronuclear MyopathyCentral Core Disease+5 more
Boston Children's Hospital4,000 enrolled1 locationNCT00272883
Recruiting
Advanced SPinal Innovations With Robotics and Enabling Technology Registry
SpondylolisthesisAdolescent Idiopathic ScoliosisCongenital Scoliosis+3 more
Boston Children's Hospital700 enrolled10 locationsNCT05071144
Recruiting
Not Applicable
COMPASSION S3 - Evaluation of the SAPIEN 3 Transcatheter Heart Valve in Patients With Pulmonary Valve Dysfunction
Complex Congenital Heart DefectDysfunctional RVOT ConduitPulmonary Valve Insufficiency+1 more
Edwards Lifesciences108 enrolled25 locationsNCT02744677
Recruiting
Project: Every Child for Younger Patients With Cancer
Malignant Solid NeoplasmNeuroendocrine NeoplasmCentral Nervous System Neoplasm+15 more
Children's Oncology Group75,000 enrolled278 locationsNCT02402244
Recruiting
Phase 1Phase 2
A Study of DB-OTO, an Adeno-Associated Virus (AAV) Based Gene Therapy, in Children/Infants With Hearing Loss Due to Otoferlin Mutations
Congenital Hearing Loss Secondary to Biallelic Mutations of the Otoferlin Gene (OTOF)
Regeneron Pharmaceuticals30 enrolled15 locationsNCT05788536
Recruiting
Extracellular Vesicle Micro RNA Profiling in Congenital Heart Disease: Fetal-Maternal Regulation in Neonatal Thrombosis
Congenital Heart Disease
Boston Children's Hospital10 enrolled1 locationNCT06434207
Recruiting
Phase 2
A Study to Evaluate Tabelecleucel in Participants With Epstein Barr Virus (EBV) Associated Diseases
LeiomyosarcomaSolid Organ Transplant ComplicationsLymphoproliferative Disorders+8 more
Pierre Fabre Medicament190 enrolled40 locationsNCT04554914
Recruiting
Genetic Studies of Strabismus, Congenital Cranial Dysinnervation Disorders (CCDDs), and Their Associated Anomalies
Facial PalsyCongenital Fibrosis of Extraocular MusclesDuane Retraction Syndrome+23 more
Boston Children's Hospital20,000 enrolled1 locationNCT03059420
Recruiting
Phase 4
De-implementing Inhaled Nitric Oxide for Congenital Diaphragmatic Hernia
Congenital Diaphragmatic Hernia
The University of Texas Health Science Center, Houston600 enrolled19 locationsNCT05213676
Recruiting
Evaluation of Pro-Inflammatory Leukocyte Activity in Patients Undergoing Cardiac Surgery
CoagulationCongenital Heart Disease
Boston Children's Hospital100 enrolled1 locationNCT04299828
Recruiting
Genetic Studies of Strabismus, Nystagmus, and Associated Disorders
StrabismusNystagmus, Congenital
Boston Children's Hospital400 enrolled1 locationNCT04770519
Recruiting
The Myelin Disorders Biorepository Project
AdrenoleukodystrophyCockayne SyndromeRefsum Disease+63 more
Children's Hospital of Philadelphia12,000 enrolled23 locationsNCT03047369
Recruiting
Clinical and Basic Investigations Into Congenital Disorders of Glycosylation
Congenital Disorders of Glycosylation
Icahn School of Medicine at Mount Sinai500 enrolled12 locationsNCT04199000
Recruiting
Phase 2
Ascending Doses of Crofelemer Powder for Oral Solution in Pediatric Microvillus Inclusion Disease (MVID)
Rare DiseasesCongenital DisordersMicrovillus Inclusion Disease
Napo Pharmaceuticals, Inc.12 enrolled3 locationsNCT06721871
Recruiting
Atrial Late Gadolinium Enhancement in Patients with Repaired Congenital Heart Disease
Congenital Heart DiseaseFibrosis MyocardialFibrosis; Heart
Boston Children's Hospital50 enrolled1 locationNCT05241418
Recruiting
Identification of Biomarkers for Patients with Vascular Anomalies
Vascular AnomalyKlippel Trenaunay SyndromeKaposiform Hemangioendothelioma+4 more
Children's Hospital Medical Center, Cincinnati1,000 enrolled2 locationsNCT03001180
Recruiting
Not Applicable
The Relationship Between Brain MRI Phenotypes, Genes and Cognitive Outcome in CHD Adults
Congenital Heart Disease
Boston Children's Hospital225 enrolled1 locationNCT05258981