Congenital Clinical Trials in Philadelphia, Pennsylvania

17 recruitingPhiladelphia, Pennsylvania

Showing 117 of 17 trials

Recruiting

ARPKD Database Study

Autosomal Recessive Polycystic Kidney DiseaseNephronophthisisCongenital Hepatic Fibrosis+7 more
Children's Hospital of Philadelphia200 enrolled6 locationsNCT01401998
Recruiting
Phase 2Phase 3

A Study in Pediatric Participants With Congenital Adrenal Hyperplasia (Balance-CAH)

Congenital Adrenal HyperplasiaClassic Congenital Adrenal Hyperplasia
Crinetics Pharmaceuticals Inc.153 enrolled35 locationsNCT07159841
Recruiting
Phase 3

Study to Evaluate Sepofarsen in Subjects With Leber Congenital Amaurosis (LCA) Type 10 (HYPERION)

Sensation DisordersLeber Congenital AmaurosisRetinal Disease+7 more
Laboratoires Thea32 enrolled16 locationsNCT06891443
Recruiting

A Natural History Study in Participants With Congenital Myasthenic Syndromes (CMS) Due to Mutations in DOK7, MUSK, AGRN, or LRP4

Congenital Myasthenic Syndrome
argenx100 enrolled30 locationsNCT06078553
Recruiting

Project: Every Child for Younger Patients With Cancer

Malignant Solid NeoplasmNeuroendocrine NeoplasmCentral Nervous System Neoplasm+15 more
Children's Oncology Group75,000 enrolled278 locationsNCT02402244
Recruiting
Not Applicable

A Pragmatic Clinical Trial of the WE BEAT Well-Being Education Program in Adolescent Congenital Heart Disease: WE BEAT CHD Study

Telemedicine-Based EducationResilience,PsychologicalPatient-Reported Outcome Measures (PROMs)+3 more
Carelon Research390 enrolled14 locationsNCT07525843
Recruiting

International Study of Cerebral Oxygenation and Electrical Activity During Major Neonatal Surgery

Neonatal surgeryCongenital DisordersCerebral Desaturation
Children's Hospital of Philadelphia900 enrolled15 locationsNCT05673499
Recruiting
Not Applicable

Fontan Fitness Trial

Congenital Heart DiseaseSingle Ventricle
Children's Hospital of Philadelphia200 enrolled1 locationNCT06918795
Recruiting

Outcomes and Health Care Resource Utilization in Pediatric Congenital Heart Disease Patients Undergoing Non-Cardiac Procedures

Congenital Heart Disease in Children
Boston Children's Hospital10,000 enrolled10 locationsNCT04604418
Recruiting
Phase 2

Study to Evaluate Ultevursen in Subjects With Retinitis Pigmentosa (RP) Due to Mutations in Exon 13 of the USH2A Gene

deaf-blindRetinitis pigmentosa (RP)Retinal Disease+4 more
Laboratoires Thea81 enrolled27 locationsNCT06627179
Recruiting
Not Applicable

COMPASSION S3 - Evaluation of the SAPIEN 3 Transcatheter Heart Valve in Patients With Pulmonary Valve Dysfunction

Complex Congenital Heart DefectDysfunctional RVOT ConduitPulmonary Valve Insufficiency+1 more
Edwards Lifesciences108 enrolled25 locationsNCT02744677
Recruiting

The Myelin Disorders Biorepository Project

AdrenoleukodystrophyCockayne SyndromeRefsum Disease+63 more
Children's Hospital of Philadelphia12,000 enrolled23 locationsNCT03047369
Recruiting

Clinical and Basic Investigations Into Congenital Disorders of Glycosylation

Congenital Disorders of Glycosylation
Icahn School of Medicine at Mount Sinai500 enrolled12 locationsNCT04199000
Recruiting
Not Applicable

Cord Clamping Among Neonates With Congenital Heart Disease

Congenital Heart Disease (CHD)
Carl Backes, MD500 enrolled21 locationsNCT06153459
Recruiting
Not Applicable

Safety and Efficacy of FETO in CDH: A Phase III Trial

Congenital Diaphragmatic HerniaPulmonary Hypoplasia
Holly L Hedrick, MD80 enrolled2 locationsNCT06884423
Recruiting
Phase 2

HM15136 (Efpegerglucagon) Treatment for 8 Weeks in Subjects Aged ≥2 Years With Congenital Hyperinsulinism (CHI)

Congenital Hyperinsulinism
Hanmi Pharmaceutical Company Limited16 enrolled7 locationsNCT04732416
Recruiting

Neurocognition in Congenital Central Hypoventilation Syndrome (CCHS)

Congenital Central Hypoventilation SyndromeCongenital Central HypoventilationCCHS+3 more
Debra Weese-Mayer1,000 enrolled4 locationsNCT03568669