HIES Clinical Trials in Philadelphia, Pennsylvania
15 recruitingPhiladelphia, Pennsylvania
Showing 1–15 of 15 trials
Recruiting
Phase 3
Acoramidis Transthyretin Amyloidosis Prevention Trial in the Young (ACT-EARLY) Study in Asymptomatic Carriers of a Pathogenic TTR Variant
CardiomyopathiesAmyloidosisHeart Diseases+3 more
Eidos Therapeutics, a BridgeBio company587 enrolled101 locationsNCT06563895
Recruiting
Early Phase 1
Study of Biodistribution, Metabolism, Excretion and Brain Uptake11C-M503
Tauopathies
University of Pennsylvania70 enrolled3 locationsNCT06303921
Recruiting
Phase 1Phase 2
Phase 1/2: CD45RA Depleted Stem Cell Addback to Prevent Viral or Fungal Infections Post TCRab/CD19 Depleted HSCT
LeukemiaInborn Errors of MetabolismHLH+11 more
Children's Hospital of Philadelphia100 enrolled1 locationNCT06839456
Recruiting
Phase 4
The PIVATAL Study -Study of Ventricular Arrhythmia (VTA) Ablation in Left Ventricular Assist Device (LVAD) Patients
CardiomyopathiesArrythmia
University of Rochester100 enrolled19 locationsNCT05034432
Recruiting
Transformative Research in Diabetic Nephropathy
Diabetic NephropathiesDiabetic Glomerulosclerosis
University of Pennsylvania400 enrolled17 locationsNCT02986984
Recruiting
Transformative Research in Diabetic Nephropathy 2.0
Diabetes Mellitus, Type 2Kidney DiseasesDiabetic Nephropathies+1 more
University of Pennsylvania200 enrolled1 locationNCT07444203
Recruiting
Phase 1
Validation of Oxygen Nanosensor in Mitochondrial Myopathy
Mitochondrial DiseasesMItochondrial Myopathies
Children's Hospital of Philadelphia24 enrolled1 locationNCT04086329
Recruiting
Phase 1
Validation of Nanosensor Oxygen Measurement
Mitochondrial diseaseMItochondrial Myopathies
Children's Hospital of Philadelphia96 enrolled1 locationNCT06819683
Recruiting
Not Applicable
CW2IP2: Imaging and Diagnostic Assessments
Tauopathies
University of Pennsylvania94 enrolled1 locationNCT06083467
Recruiting
Early Phase 1
Study of Biodistribution, Metabolism, Excretion and Brain Uptake 18F-JSS20-183A
Tauopathies
University of Pennsylvania90 enrolled2 locationsNCT06932809
Recruiting
Early Phase 1
Study of Biodistribution, Metabolism, Excretion and Brain Uptake of 11C-HY-2-15
Tauopathies
University of Pennsylvania70 enrolled1 locationNCT06032026
Recruiting
Phase 1
Applying pGz in Mitochondrial Disease
Mitochondrial DiseasesMItochondrial Myopathies
Children's Hospital of Philadelphia90 enrolled1 locationNCT05569122
Recruiting
The Myelin Disorders Biorepository Project
AdrenoleukodystrophyCockayne SyndromeRefsum Disease+63 more
Children's Hospital of Philadelphia12,000 enrolled23 locationsNCT03047369
Recruiting
Not Applicable
Using the EHR to Advance Genomic Medicine Across a Diverse Health System
ParagangliomaPheochromocytomaGenetic Predisposition+7 more
University of Pennsylvania1,000 enrolled1 locationNCT06377033
Recruiting
TRANSPIRE: Lung Injury in a Longitudinal Cohort of Pediatric HSCT Patients
Hematopoietic Stem Cell Transplant (HSCT)Thrombotic MicroangiopathiesDiffuse Alveolar Hemorrhage+2 more
Children's Hospital Medical Center, Cincinnati2,000 enrolled9 locationsNCT04098445