RecruitingPhase 1Phase 2NCT06839456

Phase 1/2: CD45RA Depleted Stem Cell Addback to Prevent Viral or Fungal Infections Post TCRab/CD19 Depleted HSCT

Phase 1/2 Study: CD45RA Depleted Peripheral Stem Cell Addback to Prevent Viral and Fungal Infections Following Alternative Donor TCRab/CD19 Depleted Hematopoietic Stem Cell Transplant


Sponsor

Children's Hospital of Philadelphia

Enrollment

100 participants

Start Date

Mar 21, 2025

Study Type

INTERVENTIONAL

Conditions

Summary

The major morbidities of allogeneic hematopoietic stem cell transplant (HSCT) using donors that are not human leukocyte antigen (HLA) matched siblings are graft vs host disease (GVHD) and life- threatening infections. T cell receptor alpha beta (TCRαβ) T lymphocyte depletion and CD19+ B lymphocyte depletion of alternative donor hematopoietic stem cell (HSC) grafts is effective in preventing GVHD, but immune reconstitution may be delayed, increasing the risk of infections. The central hypothesis of this study is that an addback of CD45RO memory T lymphocytes, derived from a fraction of the original donor peripheral stem cell product depleted of CD45RA naïve T lymphocytes, will accelerate immune reconstitution and help decrease the risk of infections in TCRab/CD19 depleted PSCT.


Eligibility

Min Age: 1 MonthMax Age: 25 Years

Plain Language Summary

Simplified for easier understanding

This study is testing a method to prevent dangerous viral infections in children and young adults who receive stem cell transplants for blood cancers or other serious blood diseases. After a transplant, the immune system takes time to rebuild, leaving patients vulnerable to life-threatening viral infections. This approach involves adding back a specific set of immune cells (CD45RA-depleted stem cells from the donor) to help the immune system recover more quickly while reducing the risk of graft-versus-host disease. **You may be eligible if...** - You are 25 years old or younger - You have a blood cancer or serious blood disease that could be cured by a stem cell transplant - A suitable donor is available for peripheral blood stem cell donation - You have adequate organ function and overall health - A parent or guardian can provide consent (or you can consent yourself if 18+) **You may NOT be eligible if...** - Your general health score (performance score) is below 60 - There is no suitable donor available - You have Hodgkin lymphoma - You are pregnant Talk to your doctor to see if this trial is right for you.

This summary was AI-generated to explain the trial in plain language. It is not medical advice. Always discuss eligibility with your doctor before enrolling in a clinical trial.

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Interventions

DEVICEPhase 1 Dose Level 1

Patients in the first dose level for the CD45RA depleted addback will receive 1 X 10\^6 CD45RO+ T cells/kg. Once all patients in this dose group have been evaluated for acute GVHD at day 100, then we will advance to the next dose level if indicated by safety analysis.

DEVICEPhase 1 Dose Level 2

Patients in the second dose level for the CD45RA depleted addback will receive 2 X 10\^6 CD45RO+ T cells/kg. Once all patients in this dose group have been evaluated for acute GVHD at day 100, then we will advance to the next dose level if indicated by safety analysis.

DEVICEPhase 1 Dose Level 3

Patients in the third and final dose level for the CD45RA depleted addback will receive 5 X 10\^6 CD45RO+ T cells/kg. All patients in this dose group will be evaluated for acute GVHD at day 100. Based on these findings, the maximum tolerated dose (MTD) will be determined. Once MTD for the addback cell dose has been determined in Phase 1, subjects with mismatched related donors will then enroll in Phase 2.

DEVICEPhase 2 Maximum Tolerated Dose determined in Phase 1

Patients with mismatched related donors will receive the CD45RA depleted addback at the maximum tolerated dose determined in the Phase 1 portion of the study.

DEVICEPhase 2 Established Dose from prior study, NCT03810196

Patients with unrelated donors will receive the CD45RA depleted addback at the dose 5 X 10\^6 CD45RO+ T cells.


Locations(1)

Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, United States

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NCT06839456


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