LMA Clinical Trials in Boston, Massachusetts
6 recruitingBoston, Massachusetts
Showing 1–6 of 6 trials
Recruiting
Phase 3
REVEAL: A Phase 3 Study of ION582 in Angelman Syndrome
Angelman Syndrome
Ionis Pharmaceuticals, Inc.158 enrolled38 locationsNCT06914609
Recruiting
Phase 1Phase 2
A Phase 1/2 Study of the Safety and Efficacy of MVX-220 in Angelman Syndrome
Angelman Syndrome
MavriX Bio, LLC12 enrolled3 locationsNCT07181837
Recruiting
Lysosomal Acid Lipase (LAL) Deficiency Registry
Lysosomal Acid Lipase DeficiencyWolman DiseaseCholesterol Ester Storage Disease+4 more
Alexion Pharmaceuticals, Inc.300 enrolled104 locationsNCT01633489
Recruiting
Phase 1Phase 2
HALOS: A Safety, Tolerability, Pharmacokinetics and Pharmacodynamics Study of Multiple Ascending Doses of ION582 in Participants With Angelman Syndrome
Angelman Syndrome
Ionis Pharmaceuticals, Inc.70 enrolled11 locationsNCT05127226
Recruiting
The Molecular Basis of Inherited Reproductive Disorders
Kallmann SyndromeHypogonadotropic HypogonadismReproductive Disorder+1 more
Stephanie B. Seminara, MD600 enrolled1 locationNCT05971836
Recruiting
Angelman Syndrome Natural History Study
Angelman Syndrome
Boston Children's Hospital300 enrolled11 locationsNCT04507997