LMA Clinical Trials in Los Angeles, California
5 recruitingLos Angeles, California
Showing 1–5 of 5 trials
Recruiting
Phase 3
REVEAL: A Phase 3 Study of ION582 in Angelman Syndrome
Angelman Syndrome
Ionis Pharmaceuticals, Inc.158 enrolled38 locationsNCT06914609
Recruiting
Phase 2
A Safety and Efficacy Study of GTX-102 in Subjects With Deletion- or Nondeletion-type Angelman Syndrome (AS)
Angelman Syndrome
Ultragenyx Pharmaceutical Inc60 enrolled22 locationsNCT07157254
Recruiting
Phase 1Phase 2
A Phase 1/2 Study of the Safety and Efficacy of MVX-220 in Angelman Syndrome
Angelman Syndrome
MavriX Bio, LLC12 enrolled3 locationsNCT07181837
Recruiting
Phase 1Phase 2
An Extension Study to Evaluate the Long-Term Safety and Clinical Activity of mRNA-3705 in Participants Previously Enrolled in Other Clinical Studies of mRNA-3705
Methylmalonic Acidemia
ModernaTX, Inc.56 enrolled12 locationsNCT05295433
Recruiting
Angelman Syndrome Natural History Study
Angelman Syndrome
Boston Children's Hospital300 enrolled11 locationsNCT04507997