Pick Disease Clinical Trials

1 recruiting

Pick Disease Trials at a Glance

8 actively recruiting trials for pick disease are listed on ClinicalTrialsFinder across 6 cities in 8 countries. The largest study group is Not Applicable with 1 trial, with the heaviest enrollment activity in Bethesda, Bern, and Austin. Lead sponsors running pick disease studies include Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD), Center for Eye Research Australia, and Bastyr University.

Browse pick disease trials by phase

Treatments under study

About Pick Disease Clinical Trials

Looking for clinical trials for Pick Disease? There are currently 1 studies actively recruiting participants. Clinical trials offer access to new treatments before they are widely available, and every approved therapy in use today was first tested through a clinical trial.

Below you can browse trials, sign up for alerts when new Pick Disease trials open, and view eligibility criteria for each study. Each listing includes the study phase, locations, and enrollment details.

Frequently Asked Questions

Common questions about Pick Disease clinical trials

A clinical trial is a carefully designed research study that tests new medical treatments, drugs, devices, or approaches in human volunteers. Every approved medication and treatment available today was proven safe and effective through clinical trials.

All clinical trials are reviewed and approved by Institutional Review Boards (IRBs) — independent committees that evaluate patient safety. Trials follow strict protocols, and your health is monitored closely throughout. You can withdraw at any time.

Not necessarily. Many trials compare the new treatment against the current standard of care, meaning all participants receive active treatment. When placebos are used, they are typically combined with standard treatment, not given alone. The trial description will always specify the design.

Under the Affordable Care Act, most private insurers are required to cover routine patient care costs during a clinical trial. The sponsor typically covers the investigational treatment itself. Medicare also covers routine costs for qualifying trials.

Yes. Participation is completely voluntary. You can withdraw at any time, for any reason, without it affecting your access to standard medical care.

Each trial has specific eligibility criteria — including age, diagnosis, disease stage, prior treatments, and general health. Browse the trials listed above and check their eligibility sections. You can also contact the trial site directly to discuss your situation.

Showing 18 of 8 trials

Recruiting

Evaluation of Biochemical Markers and Clinical Investigation of Niemann-Pick Disease, Type C

Niemann-Pick Disease, Type C
Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)900 enrolled1 locationNCT00344331
Recruiting

Establishment of Genomic and Phenotypic Database for Niemann-Pick Disease, Type C

Niemann-Pick Disease, Type C
Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)100 enrolled1 locationNCT05588167
Recruiting
Not Applicable

Retinal Hyperspectral Imaging in Neurodegenerative Diseases

DementiaAlzheimer DiseaseParkinson Disease+5 more
Center for Eye Research Australia930 enrolled1 locationNCT07545473
Recruiting
Phase 3

A Pivotal Study of N-Acetyl-L-Leucine on Niemann-Pick Disease Type C

Niemann-Pick Disease, Type C
IntraBio Inc53 enrolled14 locationsNCT05163288
Recruiting

Longitudinal Study of Neurodegenerative Disorders

Gaucher DiseaseBatten DiseaseLeukodystrophy+24 more
University of Pittsburgh1,500 enrolled1 locationNCT03333200
Recruiting

A Real-world Long-term Safety and Immunogenicity Study of Olipudase Alfa Therapy in Pediatric Patients Less Than 2 Years of Age With Acid Sphingomyelinase Deficiency (ASMD)

Niemann-Pick Diseases
Sanofi10 enrolled5 locationsNCT06192576
Recruiting
Phase 1

UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells

Batten DiseaseAdrenoleukodystrophyPelizaeus-Merzbacher Disease+9 more
Joanne Kurtzberg, MD40 enrolled1 locationNCT02254863
Recruiting

Modifiable Variables in Parkinsonism (MVP)

Corticobasal DegenerationDementia With Lewy BodiesProgressive Supranuclear Palsy+6 more
Bastyr University2,000 enrolled1 locationNCT02194816