Ataxia Clinical Trials

10 recruiting

Ataxia Trials at a Glance

57 actively recruiting trials for ataxia are listed on ClinicalTrialsFinder across 6 cities in 24 countries. The largest study group is Not Applicable with 21 trials, with the heaviest enrollment activity in Paris, Philadelphia, and Innsbruck. Lead sponsors running ataxia studies include Biogen, Assistance Publique - Hôpitaux de Paris, and Boston Children's Hospital.

Browse ataxia trials by phase

Treatments under study

About Ataxia Clinical Trials

Looking for clinical trials for Ataxia? There are currently 10 studies actively recruiting participants. Clinical trials offer access to new treatments before they are widely available, and every approved therapy in use today was first tested through a clinical trial.

Below you can browse trials, sign up for alerts when new Ataxia trials open, and view eligibility criteria for each study. Each listing includes the study phase, locations, and enrollment details.

Frequently Asked Questions

Common questions about Ataxia clinical trials

A clinical trial is a carefully designed research study that tests new medical treatments, drugs, devices, or approaches in human volunteers. Every approved medication and treatment available today was proven safe and effective through clinical trials.

All clinical trials are reviewed and approved by Institutional Review Boards (IRBs) — independent committees that evaluate patient safety. Trials follow strict protocols, and your health is monitored closely throughout. You can withdraw at any time.

Not necessarily. Many trials compare the new treatment against the current standard of care, meaning all participants receive active treatment. When placebos are used, they are typically combined with standard treatment, not given alone. The trial description will always specify the design.

Under the Affordable Care Act, most private insurers are required to cover routine patient care costs during a clinical trial. The sponsor typically covers the investigational treatment itself. Medicare also covers routine costs for qualifying trials.

Yes. Participation is completely voluntary. You can withdraw at any time, for any reason, without it affecting your access to standard medical care.

Each trial has specific eligibility criteria — including age, diagnosis, disease stage, prior treatments, and general health. Browse the trials listed above and check their eligibility sections. You can also contact the trial site directly to discuss your situation.

Showing 120 of 57 trials

Recruiting
Phase 1

A Study of SGT-212 Gene Therapy in Friedreich's Ataxia

Friedreich's Ataxia (FA)
Solid Biosciences Inc.10 enrolled3 locationsNCT07180355
Recruiting

Efficacy of Omaveloxolone Treatment for Dysphagia in French Patients With Friedreich's Ataxia

Friedreich Ataxia
Centre Hospitalier Universitaire de Nice40 enrolled1 locationNCT07013292
Recruiting

A Study to Learn More About the Long-Term Safety of BIIB141 (Omaveloxolone) in Participants With Friedreich's Ataxia Who Are Prescribed it by Their Own Doctors

Friedreich Ataxia
Biogen300 enrolled14 locationsNCT06623890
Recruiting

Clinical Course Of Disease In Participants With FA-CM

CardiomyopathyFriedreich Ataxia
Lexeo Therapeutics65 enrolled14 locationsNCT06865482
Recruiting

Patient-reported, Health Economic and Psychosocial Outcomes in Friedreich Ataxia

Friedreich Ataxia
German Center for Neurodegenerative Diseases (DZNE)200 enrolled6 locationsNCT05943002
Recruiting

Spinocerebellar Ataxia Type 27B Natural History Study (SCA27B-NHS)

Spinocerebellar Ataxia Type 27B
University Hospital Tuebingen300 enrolled5 locationsNCT06472557
Recruiting

RFC1 Natural History Study

Ataxia
Prof. Dr. Matthis Synofzik150 enrolled10 locationsNCT05177809
Recruiting
Phase 1

Phase IA and IB Study of AAVrh.10hFXN Gene Therapy for the Cardiomyopathy of Friedreich's Ataxia

CardiomyopathiesFriedreich AtaxiaMyocardial Fibrosis+1 more
Weill Medical College of Cornell University25 enrolled1 locationNCT05302271
Recruiting

Friedreich Ataxia Nerve Ultrasund

Friedreich Ataxia
Centre Hospitalier Universitaire de Nice14 enrolled1 locationNCT07508631
Recruiting
Not Applicable

Vibrotactile Balance Belt Effect on Improving Gait

Ataxia - OtherVestibular Hypofunction
Johns Hopkins University90 enrolled2 locationsNCT07253532
Recruiting
Phase 2

An Open-Label Study of CTI-1601 in Subjects With Friedreich's Ataxia

Friedreich Ataxia
Larimar Therapeutics, Inc.85 enrolled8 locationsNCT06447025
Recruiting

A Retrospective Survey-based Multicenter Study to Delineate the Molecular and Phenotypic Spectrum of Epilepsy-dyskinesia Syndromes

EpilepsyMovement DisordersNeurologic Disorder+7 more
Boston Children's Hospital500 enrolled1 locationNCT06585605
Recruiting
Not Applicable

Deep Brain Stimulation for Spinocerebellar Ataxia

Spinocerebellar Ataxia Type 6Spinocerebellar Ataxia (SCA)
University of California, San Francisco5 enrolled2 locationsNCT07288437
Recruiting

Registry and Natural History Study for Progressive Myoclonus Epilepsy Type 1 (EPM1)

Progressive Epilepsy and/or Ataxia With Myoclonus as a Major FeatureProgressive Myoclonus Epilepsy Type 1EPM1+5 more
Boston Children's Hospital200 enrolled1 locationNCT06593951
Recruiting
Phase 3

A Study to Learn More About the Effects and Long-Term Safety of BIIB141 (Omaveloxolone) in Participants With Friedreich's Ataxia Aged 2 to 15 Years Old (BRAVE)

Friedreich Ataxia
Biogen255 enrolled34 locationsNCT06953583
Recruiting
Not Applicable

Cerebellar Deep Brain Stimulation for the Treatment of Ataxia

Ataxia, Gait
University Health Network, Toronto12 enrolled1 locationNCT07427563
Recruiting
Not Applicable

Effects of a Supervised Rehabilitation Program on Disease Severity in Spastic Ataxias

Autosomal Recessive Spastic Ataxia of Charlevoix-SaguenaySpastic Paraplegia 7
Laval University84 enrolled5 locationsNCT06261424
Recruiting
Not Applicable

Effects of Cerebellar tACS-iTBS in Ataxia

Ataxia
I.R.C.C.S. Fondazione Santa Lucia30 enrolled1 locationNCT06420271
Recruiting
Not Applicable

At Home Use of Stimulation Suits for Managing MS Symptoms

Multiple SclerosisSpasticityAtaxia - Other+5 more
Daphne Kos70 enrolled2 locationsNCT07202195
Recruiting
Phase 1

Study of ARO-ATXN2 Injection in Adults With Spinocerebellar Ataxia Type 2

Spinocerebellar Ataxia Type 2
Arrowhead Pharmaceuticals36 enrolled16 locationsNCT06672445