Phase 2 Cystic Fibrosis Clinical Trials
24 recruitingPhase 2
What is a Phase 2 trial?
Phase 2 trials evaluate whether a treatment works for a specific condition and further assess its safety. These studies typically enroll several hundred participants and provide preliminary data on effectiveness.
Showing 1–20 of 24 trials
Recruiting
Phase 2
A Study to Access Activity and Safety With SAR445399 Compared With Placebo in Participants Aged 18 to 80 Years of Age With Non-Cystic Fibrosis Bronchiectasis
Non-cystic Fibrosis Bronchiectasis
Sanofi70 enrolled3 locationsNCT07547436
Recruiting
Phase 2
Phase 2 Study to Assess the Safety and Efficacy of ANG003
Cystic Fibrosis (CF)Exocrine Pancreatic Insufficiency (EPI)
Anagram Therapeutics, Inc.113 enrolled26 locationsNCT07450547
Recruiting
Phase 2
GLP-1 Agonist Therapy in Cystic Fibrosis-Related Glucose Intolerance
Cystic FibrosisDiabetesPancreatic Insufficiency+1 more
University of Pennsylvania30 enrolled2 locationsNCT04731272
Recruiting
Phase 2
Safety, Tolerability, Pharmacokinetics, and Preliminary Efficacy of SPL84 in Patients With Cystic Fibrosis
Cystic Fibrosis
SpliSense Ltd.64 enrolled3 locationsNCT06429176
Recruiting
Phase 2
A Phase II Study of Ensifentrine in Non-Cystic Fibrosis Bronchiectasis
Non-cystic Fibrosis Bronchiectasis
Verona Pharma, Inc., a subsidiary of Merck & Co., Inc. (Rahway, New Jersey USA284 enrolled51 locationsNCT06559150
Recruiting
Phase 2
Safety, Tolerability and Efficacy Study of ARCT-032 in People With Cystic Fibrosis
Cystic FibrosisCFTR Gene Mutation
Arcturus Therapeutics, Inc.33 enrolled13 locationsNCT06747858
Recruiting
Phase 2Phase 3
Maralixibat in Patients With Cystic Fibrosis and Constipation
Cystic FibrosisConstipation Chronic Idiopathic
Children's Hospital Los Angeles20 enrolled1 locationNCT06413368
Recruiting
Phase 2
Metformin for People With CFRD on CFTR Modulator Therapy to Improve Ion Channel Function
Cystic FibrosisCystic Fibrosis-related Diabetes
University of Kansas Medical Center30 enrolled1 locationNCT04530383
Recruiting
Phase 1Phase 2
A Phase 1/2 Study of VX-522 in Participants With Cystic Fibrosis (CF)
Cystic Fibrosis
Vertex Pharmaceuticals Incorporated39 enrolled43 locationsNCT05668741
Recruiting
Phase 2
4D-710 in Adult Patients With Cystic Fibrosis
Cystic Fibrosis Lung
4D Molecular Therapeutics30 enrolled20 locationsNCT05248230
Recruiting
Phase 2
Xenon-129 and Inert Fluorinated Gas Lung MRI: Study of Healthy Volunteers and Participants With Pulmonary Disease
AsthmaCystic Fibrosis
The Hospital for Sick Children30 enrolled1 locationNCT02740868
Recruiting
Phase 2
Proof-of-concept Study to Evaluate the Safety, Tolerability, Pharmacodynamics, and Pharmacokinetics of SION-719 When Added to Trikafta
Cystic Fibrosis (CF)
Sionna Therapeutics Inc.16 enrolled13 locationsNCT07108153
Recruiting
Phase 2
A Phase 2 Study Evaluating Safety and Tolerability of RCT2100 (CFTR mRNA) in Healthy Participants and in Participants With CF
Cystic Fibrosis
ReCode Therapeutics192 enrolled23 locationsNCT06237335
Recruiting
Phase 1Phase 2
A Double-Blind, Active-Controlled, Multiple-Ascending Dose Study of Aerosolized RSP-1502 in Subjects With CF and Chronic PA Lung Infection
Pseudomonas aeruginosaCystic Fibrosis LungRespiratory Infections, Recurrent, Chronic
Respirion Pharmaceuticals Pty Ltd72 enrolled22 locationsNCT06016088
Recruiting
Phase 2
Dose Range Finding, Efficacy, and Safety Study of Nebulized CSL787 in Adults With Non-cystic Fibrosis Bronchiectasis (NCFB)
Non-cystic Fibrosis Bronchiectasis
CSL Behring450 enrolled13 locationsNCT07048262
Recruiting
Phase 2
Study With Phage for CF Subjects With Pseudomonas Lung Infection
Cystic Fibrosis (CF)Chronic Pseudomonas Aeruginosa Infection
BiomX Ltd63 enrolled14 locationsNCT06998043
Recruiting
Phase 2
Targeting Inflammation With Losartan to Improve Response to Modulator Therapy in Cystic Fibrosis.
Cystic Fibrosis
University of Kansas Medical Center42 enrolled1 locationNCT06364176
Recruiting
Phase 2
A Study to Evaluate Safety and Efficacy of Subcutaneous Administration of Anakinra in Patients With CF
Cystic Fibrosis, 10011762
Heidelberg University52 enrolled3 locationsNCT03925194
Recruiting
Phase 1Phase 2
A Phase 1/2 Trial of SP-101 for the Treatment of Cystic Fibrosis (CF)
Cystic Fibrosis
Spirovant Sciences, Inc.15 enrolled4 locationsNCT06526923
Completed
Phase 2
Assessment of Citramel in Patients with Cystic Fibrosis
Cystic Fibrosis
Breathe Easy Ltd24 enrolled4 locationsACTRN12615000654550